The French compassionate programme of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del CFTR variant

The European Medicines Agency has approved the cystic fibrosis transmembrane conductance regulator (CFTR) modulator combination elexacaftor/tezacaftor/ivacaftor (ETI) for people with cystic fibrosis (CF) carrying at least one F508del variant. The United States Food and Drug Administration (FDA) also...

Celý popis

Uložené v:
Podrobná bibliografia
Vydané v:The European respiratory journal Ročník 61; číslo 5
Hlavní autori: Burgel, Pierre-Régis, Sermet-Gaudelus, Isabelle, Durieu, Isabelle, Kanaan, Reem, Macey, Julie, Grenet, Dominique, Porzio, Michele, Coolen-Allou, Nathalie, Chiron, Raphael, Marguet, Christophe, Douvry, Benoit, Dufeu, Nadine, Danner-Boucher, Isabelle, Foucaud, Pierre, Lemonnier, Lydie, Girodon, Emmanuelle, Da Silva, Jennifer, Martin, Clémence, Andrejak, Claire, Priou, Pascaline, Richaud-Thiriez, Bénédicte, Montcouquiol, Sylvie, Remus, Natacha, Fanton, Annlyse, Gachelin, Elsa, Vuillard, Constance, Audousset, Camille, Duthoit, Louise, Bellet-Fraysse, Elisabeth, Languepin, Jeanne, Nove-Josserand, Raphaele, Ohlmann, Camille, Raynaud, Quitterie, Billon, Yves, Tissot, Adrien, Leroy, Sylvie, Aubourg, Frédérique, Burnet, Espérie, Carlier, Nicolas, Fajac, Isabelle, Honoré, Isabelle, Le Bourgeois, Muriel, Le Clainche-Viala, Laurence, Corvol, Harriet, Dehillotte, Clémence, Brinchault, Graziella, Ravoninjatovo, Bruno, Le Bihan, Jean, Ramel, Sophie, Weiss, Laurence, de Miranda, Sandra, Cosson, Laure, Mankikian, Julie, Pouradier, Delphine
Médium: Journal Article
Jazyk:English
Vydavateľské údaje: England 01.05.2023
ISSN:1399-3003, 1399-3003
On-line prístup:Zistit podrobnosti o prístupe
Tagy: Pridať tag
Žiadne tagy, Buďte prvý, kto otaguje tento záznam!
Buďte prvý, kto okomentuje tento záznam!
Najprv sa musíte prihlásiť.