Safety and efficacy of the maximum tolerated dose of givinostat in polycythemia vera: a two-part Phase Ib/II study

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Vydané v:Leukemia Ročník 34; číslo 8; s. 2234 - 2237
Hlavní autori: Rambaldi, Alessandro, Iurlo, Alessandra, Vannucchi, Alessandro M, Noble, Richard, von Bubnoff, Nikolas, Guarini, Attilio, Martino, Bruno, Pezzutto, Antonio, Carli, Giuseppe, De Muro, Marianna, Luciani, Stefania, McMullin, Mary Frances, Cambier, Nathalie, Marolleau, Jean-Pierre, Mesa, Ruben A, Tibes, Raoul, Pancrazzi, Alessandro, Gesullo, Francesca, Bettica, Paolo, Manzoni, Sara, Di Tollo, Silvia
Médium: Journal Article
Jazyk:English
Vydavateľské údaje: England Nature Publishing Group 01.08.2020
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ISSN:0887-6924, 1476-5551, 1476-5551
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Author Pezzutto, Antonio
Bettica, Paolo
Manzoni, Sara
McMullin, Mary Frances
Gesullo, Francesca
Rambaldi, Alessandro
Carli, Giuseppe
Luciani, Stefania
von Bubnoff, Nikolas
Marolleau, Jean-Pierre
Guarini, Attilio
Cambier, Nathalie
Tibes, Raoul
Di Tollo, Silvia
De Muro, Marianna
Iurlo, Alessandra
Vannucchi, Alessandro M
Noble, Richard
Martino, Bruno
Pancrazzi, Alessandro
Mesa, Ruben A
Author_xml – sequence: 1
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  surname: Rambaldi
  fullname: Rambaldi, Alessandro
  email: alessandro.rambaldi@unimi.it
  organization: Department of Oncology and Hematology, University of Milan and ASST Papa Giovanni XXIII, Bergamo, Italy. alessandro.rambaldi@unimi.it
– sequence: 2
  givenname: Alessandra
  orcidid: 0000-0002-4401-0812
  surname: Iurlo
  fullname: Iurlo, Alessandra
  organization: Hematology Division, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy
– sequence: 3
  givenname: Alessandro M
  surname: Vannucchi
  fullname: Vannucchi, Alessandro M
  organization: Department of Experimental and Clinical Medicine, University of Florence, Azienda Ospedaliera-Universitaria Careggi, Florence, Italy
– sequence: 4
  givenname: Richard
  surname: Noble
  fullname: Noble, Richard
  organization: Department of Hematology, Royal Cornwall Hospital, Truro, UK
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  givenname: Nikolas
  surname: von Bubnoff
  fullname: von Bubnoff, Nikolas
  organization: Department of Hematology and Oncology, Medical Center, University of Schleswig-Holstein, Campus Lübeck, Lübeck, Germany
– sequence: 6
  givenname: Attilio
  surname: Guarini
  fullname: Guarini, Attilio
  organization: Hematology Unit, IRCCS Istituto Tumori "Giovanni Paolo II", Bari, Italy
– sequence: 7
  givenname: Bruno
  surname: Martino
  fullname: Martino, Bruno
  organization: Oncology-Hematology Department, A.O. "Bianchi-Melacrino-Morelli", Reggio Calabria, Italy
– sequence: 8
  givenname: Antonio
  orcidid: 0000-0002-3246-4470
  surname: Pezzutto
  fullname: Pezzutto, Antonio
  organization: Department of Hematology Oncology, Charité' Medical School, Campus Benjamin Franklin, Berlin, Germany
– sequence: 9
  givenname: Giuseppe
  surname: Carli
  fullname: Carli, Giuseppe
  organization: U.O. Hematology, San Bortolo Hospital, Vicenza, Italy
– sequence: 10
  givenname: Marianna
  surname: De Muro
  fullname: De Muro, Marianna
  organization: Hematology and Stem Cells Transplantation Unit, Campus Bio-Medico, University Hospital, Rome, Italy
– sequence: 11
  givenname: Stefania
  surname: Luciani
  fullname: Luciani, Stefania
  organization: U.O. Clinical Hematology, Presidio Ospedaliero "Spirito Santo"-A.S.L. Azienda Sanitaria Locale, Pescara, Italy
– sequence: 12
  givenname: Mary Frances
  orcidid: 0000-0002-0773-0204
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  organization: Centre for Medical Education, Queen's University Belfast, Belfast, UK
– sequence: 13
  givenname: Nathalie
  surname: Cambier
  fullname: Cambier, Nathalie
  organization: Service d'Oncologie Hématologie, Hospital Saint Vincent de Paul-GHICL Lille, Lille, France
– sequence: 14
  givenname: Jean-Pierre
  surname: Marolleau
  fullname: Marolleau, Jean-Pierre
  organization: Service d'Oncologie Hématologie Clinique, CHU Amiens-Hospital Sud, Amiens, France
– sequence: 15
  givenname: Ruben A
  surname: Mesa
  fullname: Mesa, Ruben A
  organization: Mayo Clinic Cancer Center, Scottsdale, AZ, USA
– sequence: 16
  givenname: Raoul
  surname: Tibes
  fullname: Tibes, Raoul
  organization: New York University School of Medicine & Perlmutter Cancer Center/ NYU Langone Health, New York, NY, USA
– sequence: 17
  givenname: Alessandro
  surname: Pancrazzi
  fullname: Pancrazzi, Alessandro
  organization: Department of Experimental and Clinical Medicine, University of Florence, Azienda Ospedaliera-Universitaria Careggi, Florence, Italy
– sequence: 18
  givenname: Francesca
  surname: Gesullo
  fullname: Gesullo, Francesca
  organization: Department of Experimental and Clinical Medicine, University of Florence, Azienda Ospedaliera-Universitaria Careggi, Florence, Italy
– sequence: 19
  givenname: Paolo
  surname: Bettica
  fullname: Bettica, Paolo
  organization: Clinical R&D Department, Italfarmaco S.p.A., Cinisello Balsamo, Italy
– sequence: 20
  givenname: Sara
  surname: Manzoni
  fullname: Manzoni, Sara
  organization: Clinical R&D Department, Italfarmaco S.p.A., Cinisello Balsamo, Italy
– sequence: 21
  givenname: Silvia
  surname: Di Tollo
  fullname: Di Tollo, Silvia
  organization: Clinical R&D Department, Italfarmaco S.p.A., Cinisello Balsamo, Italy
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SubjectTerms Adult
Aged
Aged, 80 and over
Blood cancer
Carbamates - adverse effects
Carbamates - therapeutic use
Female
Humans
Janus Kinase 2 - genetics
Male
Maximum Tolerated Dose
Middle Aged
Mutation
Polycythemia
Polycythemia vera
Polycythemia Vera - drug therapy
Polycythemia Vera - genetics
Polycythemia Vera - psychology
Quality of Life
Title Safety and efficacy of the maximum tolerated dose of givinostat in polycythemia vera: a two-part Phase Ib/II study
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