DNA polymorphisms at the BCL11A, HBS1L-MYB, and beta-globin loci associate with fetal hemoglobin levels and pain crises in sickle cell disease

Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical events, and early mortality. Interindividual variation in fetal hemoglobin (HbF) expression is a known and potentially heritable modifier of SCD s...

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Published in:Proceedings of the National Academy of Sciences - PNAS Vol. 105; no. 33; p. 11869
Main Authors: Lettre, Guillaume, Sankaran, Vijay G, Bezerra, Marcos André C, Araújo, Aderson S, Uda, Manuela, Sanna, Serena, Cao, Antonio, Schlessinger, David, Costa, Fernando F, Hirschhorn, Joel N, Orkin, Stuart H
Format: Journal Article
Language:English
Published: United States 19.08.2008
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ISSN:1091-6490, 1091-6490
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Abstract Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical events, and early mortality. Interindividual variation in fetal hemoglobin (HbF) expression is a known and potentially heritable modifier of SCD severity. High HbF levels are correlated with reduced morbidity and mortality. Common single nucleotide polymorphisms (SNPs) at the BCL11A and HBS1L-MYB loci have been implicated previously in HbF level variation in nonanemic European populations. We recently demonstrated an association between a BCL11A SNP and HbF levels in one SCD cohort [Uda M, et al. (2008) Proc Natl Acad Sci USA 105:1620-1625]. Here, we genotyped additional BCL11A SNPs, HBS1L-MYB SNPs, and an SNP upstream of (G)gamma-globin (HBG2; the XmnI polymorphism), in two independent SCD cohorts: the African American Cooperative Study of Sickle Cell Disease (CSSCD) and an SCD cohort from Brazil. We studied the effect of these SNPs on HbF levels and on a measure of SCD-related morbidity (pain crisis rate). We strongly replicated the association between these SNPs and HbF level variation (in the CSSCD, P values range from 0.04 to 2 x 10(-42)). Together, common SNPs at the BCL11A, HBS1L-MYB, and beta-globin (HBB) loci account for >20% of the variation in HbF levels in SCD patients. We also have shown that HbF-associated SNPs associate with pain crisis rate in SCD patients. These results provide a clear example of inherited common sequence variants modifying the severity of a monogenic disease.
AbstractList Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical events, and early mortality. Interindividual variation in fetal hemoglobin (HbF) expression is a known and potentially heritable modifier of SCD severity. High HbF levels are correlated with reduced morbidity and mortality. Common single nucleotide polymorphisms (SNPs) at the BCL11A and HBS1L-MYB loci have been implicated previously in HbF level variation in nonanemic European populations. We recently demonstrated an association between a BCL11A SNP and HbF levels in one SCD cohort [Uda M, et al. (2008) Proc Natl Acad Sci USA 105:1620-1625]. Here, we genotyped additional BCL11A SNPs, HBS1L-MYB SNPs, and an SNP upstream of (G)gamma-globin (HBG2; the XmnI polymorphism), in two independent SCD cohorts: the African American Cooperative Study of Sickle Cell Disease (CSSCD) and an SCD cohort from Brazil. We studied the effect of these SNPs on HbF levels and on a measure of SCD-related morbidity (pain crisis rate). We strongly replicated the association between these SNPs and HbF level variation (in the CSSCD, P values range from 0.04 to 2 x 10(-42)). Together, common SNPs at the BCL11A, HBS1L-MYB, and beta-globin (HBB) loci account for >20% of the variation in HbF levels in SCD patients. We also have shown that HbF-associated SNPs associate with pain crisis rate in SCD patients. These results provide a clear example of inherited common sequence variants modifying the severity of a monogenic disease.
Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical events, and early mortality. Interindividual variation in fetal hemoglobin (HbF) expression is a known and potentially heritable modifier of SCD severity. High HbF levels are correlated with reduced morbidity and mortality. Common single nucleotide polymorphisms (SNPs) at the BCL11A and HBS1L-MYB loci have been implicated previously in HbF level variation in nonanemic European populations. We recently demonstrated an association between a BCL11A SNP and HbF levels in one SCD cohort [Uda M, et al. (2008) Proc Natl Acad Sci USA 105:1620-1625]. Here, we genotyped additional BCL11A SNPs, HBS1L-MYB SNPs, and an SNP upstream of (G)gamma-globin (HBG2; the XmnI polymorphism), in two independent SCD cohorts: the African American Cooperative Study of Sickle Cell Disease (CSSCD) and an SCD cohort from Brazil. We studied the effect of these SNPs on HbF levels and on a measure of SCD-related morbidity (pain crisis rate). We strongly replicated the association between these SNPs and HbF level variation (in the CSSCD, P values range from 0.04 to 2 x 10(-42)). Together, common SNPs at the BCL11A, HBS1L-MYB, and beta-globin (HBB) loci account for >20% of the variation in HbF levels in SCD patients. We also have shown that HbF-associated SNPs associate with pain crisis rate in SCD patients. These results provide a clear example of inherited common sequence variants modifying the severity of a monogenic disease.Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical events, and early mortality. Interindividual variation in fetal hemoglobin (HbF) expression is a known and potentially heritable modifier of SCD severity. High HbF levels are correlated with reduced morbidity and mortality. Common single nucleotide polymorphisms (SNPs) at the BCL11A and HBS1L-MYB loci have been implicated previously in HbF level variation in nonanemic European populations. We recently demonstrated an association between a BCL11A SNP and HbF levels in one SCD cohort [Uda M, et al. (2008) Proc Natl Acad Sci USA 105:1620-1625]. Here, we genotyped additional BCL11A SNPs, HBS1L-MYB SNPs, and an SNP upstream of (G)gamma-globin (HBG2; the XmnI polymorphism), in two independent SCD cohorts: the African American Cooperative Study of Sickle Cell Disease (CSSCD) and an SCD cohort from Brazil. We studied the effect of these SNPs on HbF levels and on a measure of SCD-related morbidity (pain crisis rate). We strongly replicated the association between these SNPs and HbF level variation (in the CSSCD, P values range from 0.04 to 2 x 10(-42)). Together, common SNPs at the BCL11A, HBS1L-MYB, and beta-globin (HBB) loci account for >20% of the variation in HbF levels in SCD patients. We also have shown that HbF-associated SNPs associate with pain crisis rate in SCD patients. These results provide a clear example of inherited common sequence variants modifying the severity of a monogenic disease.
Author Uda, Manuela
Cao, Antonio
Sanna, Serena
Sankaran, Vijay G
Bezerra, Marcos André C
Araújo, Aderson S
Costa, Fernando F
Lettre, Guillaume
Orkin, Stuart H
Schlessinger, David
Hirschhorn, Joel N
Author_xml – sequence: 1
  givenname: Guillaume
  surname: Lettre
  fullname: Lettre, Guillaume
  email: lettre@broad.mit.edu
  organization: Program in Medical and Population Genetics, Broad Institute of MIT and Harvard, Cambridge, MA 02142, USA. lettre@broad.mit.edu
– sequence: 2
  givenname: Vijay G
  surname: Sankaran
  fullname: Sankaran, Vijay G
– sequence: 3
  givenname: Marcos André C
  surname: Bezerra
  fullname: Bezerra, Marcos André C
– sequence: 4
  givenname: Aderson S
  surname: Araújo
  fullname: Araújo, Aderson S
– sequence: 5
  givenname: Manuela
  surname: Uda
  fullname: Uda, Manuela
– sequence: 6
  givenname: Serena
  surname: Sanna
  fullname: Sanna, Serena
– sequence: 7
  givenname: Antonio
  surname: Cao
  fullname: Cao, Antonio
– sequence: 8
  givenname: David
  surname: Schlessinger
  fullname: Schlessinger, David
– sequence: 9
  givenname: Fernando F
  surname: Costa
  fullname: Costa, Fernando F
– sequence: 10
  givenname: Joel N
  surname: Hirschhorn
  fullname: Hirschhorn, Joel N
– sequence: 11
  givenname: Stuart H
  surname: Orkin
  fullname: Orkin, Stuart H
BackLink https://www.ncbi.nlm.nih.gov/pubmed/18667698$$D View this record in MEDLINE/PubMed
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References 7517723 - Blood. 1994 Jul 15;84(2):643-9
16554528 - N Engl J Med. 2006 Mar 23;354(12):1264-72
18245381 - Proc Natl Acad Sci U S A. 2008 Feb 5;105(5):1620-5
17701901 - Am J Hum Genet. 2007 Sep;81(3):559-75
8528252 - Nat Genet. 1996 Jan;12(1):58-64
18695233 - Proc Natl Acad Sci U S A. 2008 Aug 19;105(33):11595-6
18367739 - N Engl J Med. 2008 Mar 27;358(13):1362-9
18391951 - Nat Genet. 2008 May;40(5):609-15
7993409 - N Engl J Med. 1994 Jun 9;330(23):1639-44
12717432 - Nat Immunol. 2003 Jun;4(6):525-32
18195334 - Ann Intern Med. 2008 Jan 15;148(2):94-101
4063531 - Blood. 1985 Dec;66(6):1463-5
9585587 - Am J Hum Genet. 1998 Jun;62(6):1468-74
4008590 - J Chronic Dis. 1985;38(6):495-505
17592125 - Proc Natl Acad Sci U S A. 2007 Jul 3;104(27):11346-51
9287233 - N Engl J Med. 1997 Sep 11;337(11):762-9
18391952 - Nat Genet. 2008 May;40(5):575-83
2580306 - Proc Natl Acad Sci U S A. 1985 Apr;82(7):2111-4
17325259 - Diabetes. 2007 May;56(5):1460-7
18354102 - N Engl J Med. 2008 Mar 20;358(12):1240-9
17712044 - Blood. 2007 Nov 15;110(10):3624-6
18193043 - Nat Genet. 2008 Feb;40(2):161-9
18391950 - Nat Genet. 2008 May;40(5):584-91
17767159 - Nat Genet. 2007 Oct;39(10):1197-9
16934002 - PLoS Genet. 2006 Aug 25;2(8):e132
11719382 - Blood. 2001 Dec 1;98(12):3413-20
18193044 - Nat Genet. 2008 Feb;40(2):189-97
1710777 - N Engl J Med. 1991 Jul 4;325(1):11-6
References_xml – reference: 7517723 - Blood. 1994 Jul 15;84(2):643-9
– reference: 18354102 - N Engl J Med. 2008 Mar 20;358(12):1240-9
– reference: 7993409 - N Engl J Med. 1994 Jun 9;330(23):1639-44
– reference: 17325259 - Diabetes. 2007 May;56(5):1460-7
– reference: 9585587 - Am J Hum Genet. 1998 Jun;62(6):1468-74
– reference: 18193044 - Nat Genet. 2008 Feb;40(2):189-97
– reference: 8528252 - Nat Genet. 1996 Jan;12(1):58-64
– reference: 18193043 - Nat Genet. 2008 Feb;40(2):161-9
– reference: 16934002 - PLoS Genet. 2006 Aug 25;2(8):e132
– reference: 18195334 - Ann Intern Med. 2008 Jan 15;148(2):94-101
– reference: 12717432 - Nat Immunol. 2003 Jun;4(6):525-32
– reference: 18391951 - Nat Genet. 2008 May;40(5):609-15
– reference: 1710777 - N Engl J Med. 1991 Jul 4;325(1):11-6
– reference: 17767159 - Nat Genet. 2007 Oct;39(10):1197-9
– reference: 9287233 - N Engl J Med. 1997 Sep 11;337(11):762-9
– reference: 18391950 - Nat Genet. 2008 May;40(5):584-91
– reference: 2580306 - Proc Natl Acad Sci U S A. 1985 Apr;82(7):2111-4
– reference: 18367739 - N Engl J Med. 2008 Mar 27;358(13):1362-9
– reference: 18391952 - Nat Genet. 2008 May;40(5):575-83
– reference: 11719382 - Blood. 2001 Dec 1;98(12):3413-20
– reference: 17712044 - Blood. 2007 Nov 15;110(10):3624-6
– reference: 18245381 - Proc Natl Acad Sci U S A. 2008 Feb 5;105(5):1620-5
– reference: 16554528 - N Engl J Med. 2006 Mar 23;354(12):1264-72
– reference: 4008590 - J Chronic Dis. 1985;38(6):495-505
– reference: 17701901 - Am J Hum Genet. 2007 Sep;81(3):559-75
– reference: 4063531 - Blood. 1985 Dec;66(6):1463-5
– reference: 17592125 - Proc Natl Acad Sci U S A. 2007 Jul 3;104(27):11346-51
– reference: 18695233 - Proc Natl Acad Sci U S A. 2008 Aug 19;105(33):11595-6
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Snippet Sickle cell disease (SCD) is a debilitating monogenic blood disorder with a highly variable phenotype characterized by severe pain crises, acute clinical...
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StartPage 11869
SubjectTerms Adolescent
Anemia, Sickle Cell - complications
Anemia, Sickle Cell - epidemiology
Anemia, Sickle Cell - genetics
Anemia, Sickle Cell - metabolism
Carrier Proteins - genetics
Carrier Proteins - metabolism
Cohort Studies
Female
Fetal Hemoglobin - genetics
Fetal Hemoglobin - metabolism
Genes, myb - genetics
Genotype
Globins - genetics
Globins - metabolism
Humans
Male
Nuclear Proteins - genetics
Nuclear Proteins - metabolism
Pain - complications
Pain - epidemiology
Pain - genetics
Pain - metabolism
Polymorphism, Single Nucleotide - genetics
Title DNA polymorphisms at the BCL11A, HBS1L-MYB, and beta-globin loci associate with fetal hemoglobin levels and pain crises in sickle cell disease
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