ProxECAT: Proxy External Controls Association Test. A new case-control gene region association test using allele frequencies from public controls

A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individu...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Veröffentlicht in:PLoS genetics Jg. 14; H. 10; S. e1007591
Hauptverfasser: Hendricks, Audrey E., Billups, Stephen C., Pike, Hamish N. C., Farooqi, I. Sadaf, Zeggini, Eleftheria, Santorico, Stephanie A., Barroso, Inês, Dupuis, Josée
Format: Journal Article
Sprache:Englisch
Veröffentlicht: United States Public Library of Science 01.10.2018
Public Library of Science (PLoS)
Schlagworte:
ISSN:1553-7404, 1553-7390, 1553-7404
Online-Zugang:Volltext
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!
Abstract A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individual studies of complex traits and diseases are often smaller and underpowered to detect rare variant genetic associations. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in these studies. Fully utilizing these and other existing sequencing resources may increase power and could be especially useful in studies where resources to sequence additional samples are limited. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in large part due to the lack of statistical methods that can appropriately use this summary level data. Here, we present a new method to incorporate external controls in case-control analysis called ProxECAT (Proxy External Controls Association Test). ProxECAT estimates enrichment of rare variants within a gene region using internally sequenced cases and external controls. We evaluated ProxECAT in simulations and empirical analyses of obesity cases using both low-depth of coverage (7x) whole-genome sequenced controls and ExAC as controls. We find that ProxECAT maintains the expected type I error rate with increased power as the number of external controls increases. With an accompanying R package, ProxECAT enables the use of publicly available allele frequencies as external controls in case-control analysis.
AbstractList A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individual studies of complex traits and diseases are often smaller and underpowered to detect rare variant genetic associations. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in these studies. Fully utilizing these and other existing sequencing resources may increase power and could be especially useful in studies where resources to sequence additional samples are limited. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in large part due to the lack of statistical methods that can appropriately use this summary level data. Here, we present a new method to incorporate external controls in case-control analysis called ProxECAT (Proxy External Controls Association Test). ProxECAT estimates enrichment of rare variants within a gene region using internally sequenced cases and external controls. We evaluated ProxECAT in simulations and empirical analyses of obesity cases using both low-depth of coverage (7x) whole-genome sequenced controls and ExAC as controls. We find that ProxECAT maintains the expected type I error rate with increased power as the number of external controls increases. With an accompanying R package, ProxECAT enables the use of publicly available allele frequencies as external controls in case-control analysis.
A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individual studies of complex traits and diseases are often smaller and underpowered to detect rare variant genetic associations. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in these studies. Fully utilizing these and other existing sequencing resources may increase power and could be especially useful in studies where resources to sequence additional samples are limited. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in large part due to the lack of statistical methods that can appropriately use this summary level data. Here, we present a new method to incorporate external controls in case-control analysis called ProxECAT (Proxy External Controls Association Test). ProxECAT estimates enrichment of rare variants within a gene region using internally sequenced cases and external controls. We evaluated ProxECAT in simulations and empirical analyses of obesity cases using both low-depth of coverage (7x) whole-genome sequenced controls and ExAC as controls. We find that ProxECAT maintains the expected type I error rate with increased power as the number of external controls increases. With an accompanying R package, ProxECAT enables the use of publicly available allele frequencies as external controls in case-control analysis.A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individual studies of complex traits and diseases are often smaller and underpowered to detect rare variant genetic associations. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in these studies. Fully utilizing these and other existing sequencing resources may increase power and could be especially useful in studies where resources to sequence additional samples are limited. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in large part due to the lack of statistical methods that can appropriately use this summary level data. Here, we present a new method to incorporate external controls in case-control analysis called ProxECAT (Proxy External Controls Association Test). ProxECAT estimates enrichment of rare variants within a gene region using internally sequenced cases and external controls. We evaluated ProxECAT in simulations and empirical analyses of obesity cases using both low-depth of coverage (7x) whole-genome sequenced controls and ExAC as controls. We find that ProxECAT maintains the expected type I error rate with increased power as the number of external controls increases. With an accompanying R package, ProxECAT enables the use of publicly available allele frequencies as external controls in case-control analysis.
A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and playing a critical role in precision medicine. While this investment has resulted in an enormous total number of sequenced genomes, individual studies of complex traits and diseases are often smaller and underpowered to detect rare variant genetic associations. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in these studies. Fully utilizing these and other existing sequencing resources may increase power and could be especially useful in studies where resources to sequence additional samples are limited. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in large part due to the lack of statistical methods that can appropriately use this summary level data. Here, we present a new method to incorporate external controls in case-control analysis called ProxECAT (Proxy External Controls Association Test). ProxECAT estimates enrichment of rare variants within a gene region using internally sequenced cases and external controls. We evaluated ProxECAT in simulations and empirical analyses of obesity cases using both low-depth of coverage (7x) whole-genome sequenced controls and ExAC as controls. We find that ProxECAT maintains the expected type I error rate with increased power as the number of external controls increases. With an accompanying R package, ProxECAT enables the use of publicly available allele frequencies as external controls in case-control analysis. Recent investments have produced sequence data on millions of people with the number of sequenced individuals continuing to grow. Although large sequencing studies exist, most sequencing data is gathered and processed in much smaller units of hundreds to thousands of samples. These silos of data result in underpowered studies for rare-variant association of complex diseases. Existing genetic resources such as the Exome Aggregation Consortium (>60,000 exomes) and the Genome Aggregation Database (~140,000 sequenced samples) have the potential to be used as controls in rare variant studies of complex diseases and traits. However, to date, these large, publicly available genetic resources remain underutilized, or even misused, in part due to the high potential for bias caused by differences in sequencing technology and processing. Here we present a new method, Proxy External Controls Association Test (ProxECAT), to integrate sequencing data from different, previously incompatible sources. ProxECAT provides a robust approach to using publicly available sequencing data enabling case-control analysis when no or limited internal controls exist. Further, ProxECAT’s motivating insight, that readily available but often discarded information can be used as a proxy to adjust for differences in data generation, may motivate further method development in other big data technologies and platforms.
Author Zeggini, Eleftheria
Billups, Stephen C.
Pike, Hamish N. C.
Farooqi, I. Sadaf
Santorico, Stephanie A.
Hendricks, Audrey E.
Barroso, Inês
Dupuis, Josée
AuthorAffiliation 3 Department of Biostatistics and Informatics, Colorado School of Public Health, Aurora, CO, United States of America
5 Human Genetics, Wellcome Sanger Institute, Cambridge, United Kingdom
Regeneron Pharmaceuticals Inc, UNITED STATES
2 Human Medical Genetics and Genomics Program, University of Colorado-Denver, Aurora, CO, United States of America
4 University of Cambridge Metabolic Research Laboratories and NIHR Cambridge Biomedical Research Centre, Wellcome Trust-MRC Institute of Metabolic Science, Addenbrooke’s Hospital, Cambridge, United Kingdom
6 Department of Biostatistics, Boston University School of Public Health, Boston, MA, United States of America
1 Mathematical and Statistical Sciences Department, University of Colorado Denver, Denver, CO, United States of America
AuthorAffiliation_xml – name: 2 Human Medical Genetics and Genomics Program, University of Colorado-Denver, Aurora, CO, United States of America
– name: 6 Department of Biostatistics, Boston University School of Public Health, Boston, MA, United States of America
– name: 5 Human Genetics, Wellcome Sanger Institute, Cambridge, United Kingdom
– name: 3 Department of Biostatistics and Informatics, Colorado School of Public Health, Aurora, CO, United States of America
– name: 1 Mathematical and Statistical Sciences Department, University of Colorado Denver, Denver, CO, United States of America
– name: 4 University of Cambridge Metabolic Research Laboratories and NIHR Cambridge Biomedical Research Centre, Wellcome Trust-MRC Institute of Metabolic Science, Addenbrooke’s Hospital, Cambridge, United Kingdom
– name: Regeneron Pharmaceuticals Inc, UNITED STATES
Author_xml – sequence: 1
  givenname: Audrey E.
  orcidid: 0000-0002-7152-0287
  surname: Hendricks
  fullname: Hendricks, Audrey E.
– sequence: 2
  givenname: Stephen C.
  orcidid: 0000-0003-3627-0793
  surname: Billups
  fullname: Billups, Stephen C.
– sequence: 3
  givenname: Hamish N. C.
  surname: Pike
  fullname: Pike, Hamish N. C.
– sequence: 4
  givenname: I. Sadaf
  orcidid: 0000-0001-7609-3504
  surname: Farooqi
  fullname: Farooqi, I. Sadaf
– sequence: 5
  givenname: Eleftheria
  surname: Zeggini
  fullname: Zeggini, Eleftheria
– sequence: 6
  givenname: Stephanie A.
  surname: Santorico
  fullname: Santorico, Stephanie A.
– sequence: 7
  givenname: Inês
  orcidid: 0000-0001-5800-4520
  surname: Barroso
  fullname: Barroso, Inês
– sequence: 8
  givenname: Josée
  orcidid: 0000-0003-2871-3603
  surname: Dupuis
  fullname: Dupuis, Josée
BackLink https://www.ncbi.nlm.nih.gov/pubmed/30325923$$D View this record in MEDLINE/PubMed
BookMark eNp9ks1uEzEUhUeoiP7AGyCwxKabBP_OjLuoFEUBKlWCRVhbHs-d4Mixgz0D7WPwxnWaCUorxMpX9jmfz7XveXHig4eieEvwlLCKfFyHIXrtptsV-CnBuBKSvCjOiBBsUnHMT47q0-I8pTXGTNSyelWcMsyokJSdFX--xXC3mM-WV2hX3aPFXQ87LpoH38fgEpqlFIzVvQ0eLSH1UzRDHn4joxNMzF6FcghAEVY7kT4y9NmAhmT9CmnnwAHqIvwcwBsLKddhg7ZD46xBIym9Ll522iV4M64XxfdPi-X8y-T26-eb-ex2YgQt-wnrDOlya6yEupSNlF0t81LzqinbTjMhQJZGl1XVAtB8aDiveM070ZimxTW7KN7vuVsXkhpfMylKBcFEUEqy4mavaINeq220Gx3vVdBWPW6EuFI69tY4UJg3jWyBMSI73vJSN5wKRllHGiObssys6_G2odlAayA3q90T6NMTb3-oVfilSiIJrqoMuBwBMeT3S73a2GTAOe0hDDk3oYRLyrnM0g_PpP_u7t1xor9RDrORBVd7gYkhpQidMrZ__NUc0DpFsNoN4gGudoOoxkHMZv7MfOD_1_YACX_nsg
CitedBy_id crossref_primary_10_1002_gepi_22444
crossref_primary_10_1038_s41467_022_30248_0
crossref_primary_10_1016_j_ebiom_2021_103530
crossref_primary_10_1016_j_ajhg_2024_12_007
crossref_primary_10_1038_s41576_022_00487_4
crossref_primary_10_1093_bioadv_vbae128
crossref_primary_10_1093_hmg_ddab261
crossref_primary_10_1097_PR9_0000000000000826
crossref_primary_10_2147_VHRM_S330766
crossref_primary_10_1016_j_bneo_2025_100118
crossref_primary_10_1038_s41588_023_01637_y
crossref_primary_10_1371_journal_pone_0280951
crossref_primary_10_1093_nar_gkab1234
crossref_primary_10_1016_j_ajhg_2021_05_016
crossref_primary_10_1111_ahg_12464
crossref_primary_10_1093_jnci_djac151
crossref_primary_10_1111_cge_14038
crossref_primary_10_1002_gepi_22370
crossref_primary_10_1007_s12020_020_02248_x
crossref_primary_10_3390_cancers13092243
crossref_primary_10_1038_s41467_021_26114_0
crossref_primary_10_1016_j_cmet_2020_05_007
crossref_primary_10_3389_fgene_2022_1014947
crossref_primary_10_1038_s43588_025_00864_z
Cites_doi 10.1186/gb-2005-6-5-r44
10.1086/519795
10.1002/gepi.22057
10.1038/ng.2607
10.1038/nature15393
10.1371/journal.pone.0031358
10.1038/nature09534
10.1038/nature14962
10.1016/j.ajhg.2012.09.004
10.1016/j.ajhg.2013.04.015
10.1038/s41598-017-03054-8
10.1186/s13059-016-0974-4
10.1038/nature12975
10.1101/gr.094052.109
10.1073/pnas.1322563111
10.1214/aoms/1177732360
10.1038/nature19057
ContentType Journal Article
Copyright 2018 Hendricks et al. This is an open access article distributed under the terms of the Creative Commons Attribution License: http://creativecommons.org/licenses/by/4.0/ (the “License”), which permits unrestricted use, distribution, and reproduction in any medium, provided the original author and source are credited. Notwithstanding the ProQuest Terms and Conditions, you may use this content in accordance with the terms of the License.
2018 Hendricks et al 2018 Hendricks et al
Copyright_xml – notice: 2018 Hendricks et al. This is an open access article distributed under the terms of the Creative Commons Attribution License: http://creativecommons.org/licenses/by/4.0/ (the “License”), which permits unrestricted use, distribution, and reproduction in any medium, provided the original author and source are credited. Notwithstanding the ProQuest Terms and Conditions, you may use this content in accordance with the terms of the License.
– notice: 2018 Hendricks et al 2018 Hendricks et al
DBID AAYXX
CITATION
NPM
3V.
7QP
7QR
7SS
7TK
7TM
7TO
7X7
7XB
88E
8FD
8FE
8FH
8FI
8FJ
8FK
ABUWG
AFKRA
AZQEC
BBNVY
BENPR
BHPHI
CCPQU
DWQXO
FR3
FYUFA
GHDGH
GNUQQ
H94
HCIFZ
K9.
LK8
M0S
M1P
M7P
P64
PHGZM
PHGZT
PIMPY
PJZUB
PKEHL
PPXIY
PQEST
PQGLB
PQQKQ
PQUKI
PRINS
RC3
7X8
5PM
DOA
DOI 10.1371/journal.pgen.1007591
DatabaseName CrossRef
PubMed
ProQuest Central (Corporate)
Calcium & Calcified Tissue Abstracts
Chemoreception Abstracts
Entomology Abstracts (Full archive)
Neurosciences Abstracts
Nucleic Acids Abstracts
Oncogenes and Growth Factors Abstracts
Health & Medical Collection
ProQuest Central (purchase pre-March 2016)
Medical Database (Alumni Edition)
Technology Research Database
ProQuest SciTech Collection
ProQuest Natural Science Collection
Hospital Premium Collection
Hospital Premium Collection (Alumni Edition)
ProQuest Central (Alumni) (purchase pre-March 2016)
ProQuest Central (Alumni Edition)
ProQuest Central UK/Ireland
ProQuest Central Essentials
Biological Science Collection
ProQuest Central
Natural Science Collection
ProQuest One Community College
ProQuest Central Korea
Engineering Research Database
Health Research Premium Collection
Health Research Premium Collection (Alumni)
ProQuest Central Student
AIDS and Cancer Research Abstracts
SciTech Premium Collection
ProQuest Health & Medical Complete (Alumni)
ProQuest Biological Science Collection
Health & Medical Collection (Alumni Edition)
Medical Database
Biological Science Database
Biotechnology and BioEngineering Abstracts
ProQuest Central Premium
ProQuest One Academic (New)
Publicly Available Content Database
ProQuest Health & Medical Research Collection
ProQuest One Academic Middle East (New)
ProQuest One Health & Nursing
ProQuest One Academic Eastern Edition (DO NOT USE)
ProQuest One Applied & Life Sciences
ProQuest One Academic (retired)
ProQuest One Academic UKI Edition
ProQuest Central China
Genetics Abstracts
MEDLINE - Academic
PubMed Central (Full Participant titles)
DOAJ Directory of Open Access Journals
DatabaseTitle CrossRef
PubMed
Publicly Available Content Database
ProQuest Central Student
Oncogenes and Growth Factors Abstracts
Technology Research Database
ProQuest One Academic Middle East (New)
ProQuest Central Essentials
Nucleic Acids Abstracts
ProQuest Health & Medical Complete (Alumni)
ProQuest Central (Alumni Edition)
SciTech Premium Collection
ProQuest One Community College
ProQuest One Health & Nursing
ProQuest Natural Science Collection
ProQuest Central China
ProQuest Central
ProQuest One Applied & Life Sciences
ProQuest Health & Medical Research Collection
Genetics Abstracts
Health Research Premium Collection
Health and Medicine Complete (Alumni Edition)
Natural Science Collection
ProQuest Central Korea
Health & Medical Research Collection
Biological Science Collection
AIDS and Cancer Research Abstracts
Chemoreception Abstracts
ProQuest Central (New)
ProQuest Medical Library (Alumni)
ProQuest Biological Science Collection
ProQuest One Academic Eastern Edition
ProQuest Hospital Collection
Health Research Premium Collection (Alumni)
Biological Science Database
ProQuest SciTech Collection
Neurosciences Abstracts
ProQuest Hospital Collection (Alumni)
Biotechnology and BioEngineering Abstracts
Entomology Abstracts
ProQuest Health & Medical Complete
ProQuest Medical Library
ProQuest One Academic UKI Edition
Engineering Research Database
ProQuest One Academic
Calcium & Calcified Tissue Abstracts
ProQuest One Academic (New)
ProQuest Central (Alumni)
MEDLINE - Academic
DatabaseTitleList
PubMed
Publicly Available Content Database
MEDLINE - Academic


Database_xml – sequence: 1
  dbid: DOA
  name: DOAJ Directory of Open Access Journals
  url: https://www.doaj.org/
  sourceTypes: Open Website
– sequence: 2
  dbid: NPM
  name: PubMed
  url: http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?db=PubMed
  sourceTypes: Index Database
– sequence: 3
  dbid: PIMPY
  name: Publicly Available Content Database
  url: http://search.proquest.com/publiccontent
  sourceTypes: Aggregation Database
DeliveryMethod fulltext_linktorsrc
Discipline Biology
Public Health
DocumentTitleAlternate ProxECAT: A new case-control gene region association test using allele frequencies from public controls
EISSN 1553-7404
ExternalDocumentID 2251015221
oai_doaj_org_article_04bb9de3319f4d46ab425323f1bc9b66
PMC6191077
30325923
10_1371_journal_pgen_1007591
Genre Research Support, Non-U.S. Gov't
Journal Article
Research Support, N.I.H., Extramural
GeographicLocations United Kingdom--UK
United States--US
Colorado
GeographicLocations_xml – name: Colorado
– name: United Kingdom--UK
– name: United States--US
GrantInformation_xml – fundername: Wellcome Trust
  grantid: WT098051
– fundername: Wellcome Trust
  grantid: WT206194
– fundername: NIDDK NIH HHS
  grantid: U01 DK078616
– fundername: ;
  grantid: DK078616
– fundername: ;
  grantid: WT098051
– fundername: ;
  grantid: WT206194
– fundername: ;
  grantid: 1015182
GroupedDBID ---
123
29O
2WC
53G
5VS
7X7
88E
8FE
8FH
8FI
8FJ
AAFWJ
AAUCC
AAWOE
AAYXX
ABDBF
ABUWG
ACCTH
ACGFO
ACIHN
ACIWK
ACPRK
ACUHS
ADBBV
ADRAZ
AEAQA
AENEX
AFFHD
AFKRA
AFPKN
AHMBA
ALMA_UNASSIGNED_HOLDINGS
AOIJS
B0M
BAIFH
BAWUL
BBNVY
BBTPI
BCNDV
BENPR
BHPHI
BPHCQ
BVXVI
BWKFM
CCPQU
CITATION
CS3
DIK
DU5
E3Z
EAP
EAS
EBD
EBS
EJD
EMK
EMOBN
ESX
F5P
FPL
FYUFA
GROUPED_DOAJ
GX1
HCIFZ
HMCUK
HYE
IAO
IGS
IHR
IHW
INH
INR
IOV
ISN
ISR
ITC
KQ8
LK8
M1P
M48
M7P
O5R
O5S
OK1
OVT
P2P
PHGZM
PHGZT
PIMPY
PJZUB
PPXIY
PQGLB
PQQKQ
PROAC
PSQYO
PV9
QF4
QN7
RNS
RPM
RZL
SV3
TR2
TUS
UKHRP
WOW
XSB
~8M
ALIPV
C1A
H13
IPNFZ
NPM
RIG
WOQ
3V.
7QP
7QR
7SS
7TK
7TM
7TO
7XB
8FD
8FK
AZQEC
DWQXO
FR3
GNUQQ
H94
K9.
P64
PKEHL
PQEST
PQUKI
PRINS
RC3
7X8
PUEGO
5PM
-
AAPBV
ABPTK
ADACO
BBAFP
M~E
ID FETCH-LOGICAL-c526t-3fc1f40436e869b99f899b9847b6dfa355e96ca677dee2f89c447484f5bcbd083
IEDL.DBID FPL
ISICitedReferencesCount 24
ISICitedReferencesURI http://www.webofscience.com/api/gateway?GWVersion=2&SrcApp=Summon&SrcAuth=ProQuest&DestLinkType=CitingArticles&DestApp=WOS_CPL&KeyUT=000449328500006&url=https%3A%2F%2Fcvtisr.summon.serialssolutions.com%2F%23%21%2Fsearch%3Fho%3Df%26include.ft.matches%3Dt%26l%3Dnull%26q%3D
ISSN 1553-7404
1553-7390
IngestDate Fri Nov 26 17:12:52 EST 2021
Mon Nov 10 04:27:58 EST 2025
Tue Nov 04 01:48:26 EST 2025
Thu Oct 02 06:44:01 EDT 2025
Sat Nov 29 14:31:46 EST 2025
Mon Jul 21 05:58:49 EDT 2025
Sat Nov 29 01:34:24 EST 2025
Tue Nov 18 21:45:13 EST 2025
IsDoiOpenAccess true
IsOpenAccess true
IsPeerReviewed true
IsScholarly true
Issue 10
Language English
License This is an open access article distributed under the terms of the Creative Commons Attribution License, which permits unrestricted use, distribution, and reproduction in any medium, provided the original author and source are credited.
Creative Commons Attribution License
LinkModel DirectLink
MergedId FETCHMERGED-LOGICAL-c526t-3fc1f40436e869b99f899b9847b6dfa355e96ca677dee2f89c447484f5bcbd083
Notes ObjectType-Article-1
SourceType-Scholarly Journals-1
ObjectType-Feature-2
content type line 14
content type line 23
The authors have declared that no competing interests exist.
ORCID 0000-0001-7609-3504
0000-0002-7152-0287
0000-0003-2871-3603
0000-0003-3627-0793
0000-0001-5800-4520
OpenAccessLink http://dx.doi.org/10.1371/journal.pgen.1007591
PMID 30325923
PQID 2251015221
PQPubID 1436339
ParticipantIDs plos_journals_2251015221
doaj_primary_oai_doaj_org_article_04bb9de3319f4d46ab425323f1bc9b66
pubmedcentral_primary_oai_pubmedcentral_nih_gov_6191077
proquest_miscellaneous_2121492449
proquest_journals_2251015221
pubmed_primary_30325923
crossref_citationtrail_10_1371_journal_pgen_1007591
crossref_primary_10_1371_journal_pgen_1007591
PublicationCentury 2000
PublicationDate 2018-10-01
PublicationDateYYYYMMDD 2018-10-01
PublicationDate_xml – month: 10
  year: 2018
  text: 2018-10-01
  day: 01
PublicationDecade 2010
PublicationPlace United States
PublicationPlace_xml – name: United States
– name: San Francisco
– name: San Francisco, CA USA
PublicationTitle PLoS genetics
PublicationTitleAlternate PLoS Genet
PublicationYear 2018
Publisher Public Library of Science
Public Library of Science (PLoS)
Publisher_xml – name: Public Library of Science
– name: Public Library of Science (PLoS)
References GR Abecasis (ref9) 2010; 467
S Lee (ref4) 2017; 41
K Eilbeck (ref18) 2005; 6
W McLaren (ref11) 2016; 17
I Ionita-Laza (ref5) 2013; 92
E Wheeler (ref13) 2013; 45
SM Purcell (ref7) 2014; 506
M Lek (ref2) 2016; 536
AE Hendricks (ref6) 2017; 7
JC Barrett (ref3) 2017
A Auton (ref10) 2015; 526
UK Consortium (ref17) 2015; 526
S Wilks (ref8) 1938; 9
DH Alexander (ref15) 2009; 19
G Jun (ref14) 2012; 91
D Zhi (ref12) 2012; 7
S Purcell (ref16) 2007; 81
O Zuk (ref1) 2014; 111
References_xml – volume: 6
  start-page: R44
  issue: 5
  year: 2005
  ident: ref18
  article-title: The Sequence Ontology: a tool for the unification of genome annotations
  publication-title: Genome Biol
  doi: 10.1186/gb-2005-6-5-r44
– volume: 81
  start-page: 559
  issue: 3
  year: 2007
  ident: ref16
  article-title: PLINK: a tool set for whole-genome association and population-based linkage analyses
  publication-title: Am J Hum Genet
  doi: 10.1086/519795
– volume: 41
  start-page: 610
  issue: 7
  year: 2017
  ident: ref4
  article-title: Improving power for rare-variant tests by integrating external controls
  publication-title: Genet Epidemiol
  doi: 10.1002/gepi.22057
– volume: 45
  start-page: 513
  issue: 5
  year: 2013
  ident: ref13
  article-title: Genome-wide SNP and CNV analysis identifies common and low-frequency variants associated with severe early-onset obesity
  publication-title: Nature genetics
  doi: 10.1038/ng.2607
– year: 2017
  ident: ref3
  article-title: New mutations, old statistical challenges
  publication-title: bioRxiv
– volume: 526
  start-page: 68
  issue: 7571
  year: 2015
  ident: ref10
  article-title: A global reference for human genetic variation
  publication-title: Nature
  doi: 10.1038/nature15393
– volume: 7
  start-page: e31358
  issue: 2
  year: 2012
  ident: ref12
  article-title: Statistical guidance for experimental design and data analysis of mutation detection in rare monogenic mendelian diseases by exome sequencing
  publication-title: PLoS One
  doi: 10.1371/journal.pone.0031358
– volume: 467
  start-page: 1061
  issue: 7319
  year: 2010
  ident: ref9
  article-title: A map of human genome variation from population-scale sequencing
  publication-title: Nature
  doi: 10.1038/nature09534
– volume: 526
  start-page: 82
  issue: 7571
  year: 2015
  ident: ref17
  article-title: The UK10K project identifies rare variants in health and disease
  publication-title: Nature
  doi: 10.1038/nature14962
– volume: 91
  start-page: 839
  issue: 5
  year: 2012
  ident: ref14
  article-title: Detecting and estimating contamination of human DNA samples in sequencing and array-based genotype data
  publication-title: Am J Hum Genet
  doi: 10.1016/j.ajhg.2012.09.004
– volume: 92
  start-page: 841
  issue: 6
  year: 2013
  ident: ref5
  article-title: Sequence kernel association tests for the combined effect of rare and common variants
  publication-title: Am J Hum Genet
  doi: 10.1016/j.ajhg.2013.04.015
– volume: 7
  start-page: 4394
  issue: 1
  year: 2017
  ident: ref6
  article-title: Rare Variant Analysis of Human and Rodent Obesity Genes in Individuals with Severe Childhood Obesity
  publication-title: Sci Rep
  doi: 10.1038/s41598-017-03054-8
– volume: 17
  start-page: 122
  issue: 1
  year: 2016
  ident: ref11
  article-title: The Ensembl Variant Effect Predictor
  publication-title: Genome Biol
  doi: 10.1186/s13059-016-0974-4
– volume: 506
  start-page: 185
  issue: 7487
  year: 2014
  ident: ref7
  article-title: A polygenic burden of rare disruptive mutations in schizophrenia
  publication-title: Nature
  doi: 10.1038/nature12975
– volume: 19
  start-page: 1655
  issue: 9
  year: 2009
  ident: ref15
  article-title: Fast model-based estimation of ancestry in unrelated individuals
  publication-title: Genome Res
  doi: 10.1101/gr.094052.109
– volume: 111
  start-page: E455
  issue: 4
  year: 2014
  ident: ref1
  article-title: Searching for missing heritability: designing rare variant association studies
  publication-title: Proc Natl Acad Sci U S A
  doi: 10.1073/pnas.1322563111
– volume: 9
  start-page: 60
  year: 1938
  ident: ref8
  article-title: The large-sample distribution of the likelihood ratio for testing composite hypotheses
  publication-title: The Annals of Mathematical Statistics
  doi: 10.1214/aoms/1177732360
– volume: 536
  start-page: 285
  issue: 7616
  year: 2016
  ident: ref2
  article-title: Analysis of protein-coding genetic variation in 60,706 humans
  publication-title: Nature
  doi: 10.1038/nature19057
SSID ssj0035897
Score 2.4062114
Snippet A primary goal of the recent investment in sequencing is to detect novel genetic associations in health and disease improving the development of treatments and...
SourceID plos
doaj
pubmedcentral
proquest
pubmed
crossref
SourceType Open Website
Open Access Repository
Aggregation Database
Index Database
Enrichment Source
StartPage e1007591
SubjectTerms Alleles
Biology and Life Sciences
Biomedical research
Consortia
Disease
Gene frequency
Genetic resources
Genetics
Genomes
Genomics
Hypotheses
Informatics
Laboratories
Metabolism
Methods
Mutation
Obesity
Physical Sciences
Population genetics
Precision medicine
Public health
Research and Analysis Methods
Social Sciences
SummonAdditionalLinks – databaseName: DOAJ Directory of Open Access Journals
  dbid: DOA
  link: http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwrV3Pa9swFBajbLDLaLsf9dYNDXZVa0mWFPWWhZQeRukhg96Mfm6F4JQ4Leuf0f94T5YSklHoZTdjyZKl9yx9H376HkLfbFCCeicIN1yRhlFJYA30hDIWLVfRBD4cFP6hLi9H19f6aivVV4oJy_LAeeJO68Za7QMHV4mNb6Sx4GWc8Uit01YOYtu10msylddgLkY5rYoQnCig9eXQHFf0tNjo5BYMNMQICE13NqVBuz9pnc4X_VO489_wya396HwfvSlAEo_zAA7Qi9Adolc5teTDW_R4tVz8mU7GszOcrh7wtMg940kOTu_xlmXwDLo-wWMMIBs72NhICWHH8PoBp-wNUMlsPQAIdYVT0PwvnLKxzAOOyxyVDdQbp0MrOCto49JS_w79PJ_OJhekpF8gTjC5Ijw6GpP4jgwjqa3WEbiZ1WBKK300AFSCls5IpXwIDApd0yRl0iissx6g3Xu01y26cIRwVKw2biQs574JVhoffV2b2FBnQuS-Qnw9_60r2uQpRca8HX64KeAoeVbbZLW2WK1CZPPUbdbmeKb-92TaTd2krD3cAH9ri7-1z_lbhY6SY6w76FtYEGFZAxgL7R-vneXp4q-bYviG048Z04XFHdShDIgqAC1doQ_ZtzYvCRADGCrjFVI7Xrczit2S7ub3oBMO3BjIvfr4P4b9Cb0GqJiVgOkx2lst78Jn9NLdr2765Zfh4_sLP_E4Jw
  priority: 102
  providerName: Directory of Open Access Journals
– databaseName: Biological Science Database
  dbid: M7P
  link: http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwpV1db9MwFLVggISE-BiwBQYyEq9mcezYDS-oVJ14QFMfirS3yJ_bpKopSTexn8E_5jp2SosmeOCtip3UiY-vz7Wvz0XovXaypNaUhCkmCS-oIGADLaFF4TWTXjnWHxT-Kk9PR2dn1SwtuHUprHKwib2hto0Ja-THgDtAD7AF-mn1nYSsUWF3NaXQuIvuBZWEog_dmw2WmJWjmFylLBmR4Nyno3NM0uPUUx9W0E19pEBZ0Z2pqVfwD4qni6a7jX3-GUS5NSudPPnf93mKHic-iscRQM_QHbfcRw9ihsqbffQoLuvheFrpOfo5a5sf08l4_hGHXzd4mlSk8STGvHd4q8PxPLQHjzFwd2xgviQpMh7D93A4JIWASmrrBiC-axxi8c9xSPKycNi3MdgbPHoczsLgKMyN05O6F-jbyXQ--UJSVgdiykKsCfOG-qDpI9xIVLqqPLh8ugKEaGG9Av7jKmGUkNI6V0Ch4TwInvpSG22BMb5Ee8tm6Q4R9rLIlRmVmjHLnRbKepvnynNqlPPMZogNHVqbJHkeMm8s6n4fT4LrE79yHWBQJxhkiGzuWkXJj3_U_xywsqkbBLv7C017XqfxX-dc68o6BhbPc8uF0mAsWcE81abSQmToMCBt-IOu_o2PDB0NCLq9-N2mGExD2O9RS9dcQR0YExz8a15l6CCCddNIYC7g-BYsQ3IHxjtvsVuyvLzo5cfB5aa5lK_-3qzX6CFwyygdTI_Q3rq9cm_QfXO9vuzat_04_QXeZ0rj
  priority: 102
  providerName: ProQuest
Title ProxECAT: Proxy External Controls Association Test. A new case-control gene region association test using allele frequencies from public controls
URI https://www.ncbi.nlm.nih.gov/pubmed/30325923
https://www.proquest.com/docview/2251015221
https://www.proquest.com/docview/2121492449
https://pubmed.ncbi.nlm.nih.gov/PMC6191077
https://doaj.org/article/04bb9de3319f4d46ab425323f1bc9b66
http://dx.doi.org/10.1371/journal.pgen.1007591
Volume 14
WOSCitedRecordID wos000449328500006&url=https%3A%2F%2Fcvtisr.summon.serialssolutions.com%2F%23%21%2Fsearch%3Fho%3Df%26include.ft.matches%3Dt%26l%3Dnull%26q%3D
hasFullText 1
inHoldings 1
isFullTextHit
isPrint
journalDatabaseRights – providerCode: PRVAON
  databaseName: DOAJ Directory of Open Access Journals
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: DOA
  dateStart: 20050101
  isFulltext: true
  titleUrlDefault: https://www.doaj.org/
  providerName: Directory of Open Access Journals
– providerCode: PRVPQU
  databaseName: Biological Science Database
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: M7P
  dateStart: 20050701
  isFulltext: true
  titleUrlDefault: http://search.proquest.com/biologicalscijournals
  providerName: ProQuest
– providerCode: PRVPQU
  databaseName: Health & Medical Collection
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: 7X7
  dateStart: 20050701
  isFulltext: true
  titleUrlDefault: https://search.proquest.com/healthcomplete
  providerName: ProQuest
– providerCode: PRVPQU
  databaseName: ProQuest Central
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: BENPR
  dateStart: 20050701
  isFulltext: true
  titleUrlDefault: https://www.proquest.com/central
  providerName: ProQuest
– providerCode: PRVPQU
  databaseName: Publicly Available Content Database
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: PIMPY
  dateStart: 20050701
  isFulltext: true
  titleUrlDefault: http://search.proquest.com/publiccontent
  providerName: ProQuest
– providerCode: PRVATS
  databaseName: Public Library of Science (PLoS) Journals Open Access
  customDbUrl:
  eissn: 1553-7404
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0035897
  issn: 1553-7404
  databaseCode: FPL
  dateStart: 20050701
  isFulltext: true
  titleUrlDefault: http://www.plos.org/publications/
  providerName: Public Library of Science
link http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwlV3da9swEBdbu8Fg7KP7qLfOaLBXd7ZkS9be0pCwQRfMyCB7MvrcCsEpcVraP2P_8U6WkyWlZewlmJxkn0-n0511-h1CH5TlRWZ0kVBJeZKTjCVgA02SEeIU5U5a2h0UPuWTSTmbiepvoHhjB5_y7GMv0-NzEGi3p1_4w-r7hDLmg61xdbq2vLQoBe-Px93Vc2f56VD6ParpfNHe5mHeTJTcWnnGT_-X52foSe9j4kFQiufonm0O0MNQdfL6AD0On-pwOIH0Av2ulour0XAw_YT91TUe9cjQeBjy2Fu8NYh4Crwf4wEGfxxrWAOTPtsdAxcW-0IP0EhudQBndoV9fv1P7Au3zC12y5DADVE69udbcADbxv2d2pfo-3g0HX5O-koNiS4IWyXU6cx5nB5mSyaUEA7COCVg1BUzToJPYwXTknFurCVA1HnuQUxdobQy4AW-QnvNorGHCDtOUqnLQlFqcquYNM6kqXR5pqV11ESIrgew1j2Mua-mMa-7vTkO4UyQcu2FX_fCj1Cy6XUeYDz-0f7E68amrQfh7v6AUa77OV2nuVLCWApWzOUmZ1KBAaSEukxpoRiL0KHXrPUD2hpsJ1hA8Hjh_kdrbbud_H5Dhunu93BkYxcX0CYjENOCTyYi9Doo54ZJ8EYgmCU0QnxHbXfeYpfSnP3qIMUhjM5Szt_czfFb9Ah8xQAFnB2hvdXywr5DD_Tl6qxdxug-n_Hut4zR_sloUn2Lu88bcTdDY59SWwGl-vK1-vEHJnE-cw
linkProvider Public Library of Science
linkToHtml http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMw1V1bb9MwFD4aHQgkxGVcFhhgJHgMq-PEbpAQKmXTqnVVH4o0nkJ8G5WqtjQd0J_BH-E3chwnpUUTPO2Bt6p2Usf9fPyd-JzvALyQRiRUqyRkORNhHFEeog3UIY0iK5mwuWFlonBP9Put09N0sAU_61wYF1ZZ28TSUOupcu_I9xF3iB5kC_Tt7Evoqka509W6hIaHxbFZfkOXrXjTfY__78soOjwYdo7CqqpAqJKIL0JmFbVOU4abFk9lmlp0OWSKI5Rc2xz3X5NylXMhtDERNqo4doKbNpFKamQseN8rsB07sDdge9A9GXysbT9LWr6cS5KwULC0WSXrMUH3K2y8miEwytiEJKUbm2FZM8BprI6nxUV898-wzbV98PD2_zaDd-BWxbhJ2y-Ru7BlJjtwzdfgXO7ATf_ikvh8rHvwYzCffj_otIevifu0JAeVTjbp-Kj-gqxBmgzd85M2Qe-EKGQEYRX7T3D-DXFlL7BTvnYBUvsFcdkGZ8SVsRkbYuc-nH1kCuKyfYiXHifVnYr78OFS5ucBNCbTidkFYkXUzFUrkYzp2Eiea6ubzdzGVOXGMh0AqwGUqUrU3dUWGWflSaVA587PcuZgl1WwCyBcXTXzoib_6P_OYXPV10mSl19M52dZZeGyZixlqg1Dm25jHfNc4gphEbNUqlRyHsCuQ3b9A0X2G48B7NWIvbj5-aoZjZ870conZnqOfWiEHj4y1DSAh35xrAaJ3Axd-4gFIDaWzcZTbLZMRp9LgXVOkUQL8ejvw3oG14-GJ72s1-0fP4YbyKS9UDLdg8Zifm6ewFX1dTEq5k8rK0Hg02Uvq19JiqnE
linkToPdf http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMw1V1bb9MwFLZGBwgJcRmXBQYYCR5DazuxGySESteKaqPqQ5G2pxA79qhUNaXpgP4M_g6_juPYKS2a4GkPvFW1k7rOd875TnwuCL2QWsQkV3HIMibCiBIegg7MQ0KpkUyYTLMqUfhYDIftk5NktIN-1rkwNqyy1omVos4LZd-RNwF3gB5gC6RpfFjE6LD_dv4ltB2k7Elr3U7DQeRIr76B-1a-GRzCs35Jab837r4PfYeBUMWUL0NmFDG2vgzXbZ7IJDHgfsgEVit5bjKwxTrhKuNC5FpTGFRRZItvmlgqmQN7gfteQbtAySPaQLujwYfRaW0HWNx2rV3imIWCJS2fuMcEaXqcvJoDSKo4hTghW4ax6h9g661Oi_Ii7vtnCOeGTezf_p938w665Zk47jjRuYt29GwPXXO9OVd76KZ7oYldntY99GO0KL73up3xa2w_rXDP18_GXRftX-INqOOx3QvcweC1YAVMIfQ5ARiehca2HQZMyjYuAMq_xDYL4Qzb9jZTjc3ChblPdIltFhB2Jcmxv1N5H328lP15gBqzYqb3ETaCtjLVjiVjeaQlz3KTt1qZiYjKtGF5gFgNplT5Yu-258g0rU4wBTh9bpdTC8HUQzBA4fqquSt28o_57yxO13NtqfLqi2JxlnrNl7YiKZNcM9D1JsojnkkwE4wyQ6RKJOcB2rcor3-gTH9jM0AHNXovHn6-HgalaE-6spkuzmEOoeD5A3NNAvTQCcp6kcDZwOWnLEBiS4S2_sX2yGzyuSq8zgmQayEe_X1Zz9B1kKX0eDA8eoxuAMF29ZPJAWosF-f6Cbqqvi4n5eKpVxgYfbpsqfoFnvyyhA
openUrl ctx_ver=Z39.88-2004&ctx_enc=info%3Aofi%2Fenc%3AUTF-8&rfr_id=info%3Asid%2Fsummon.serialssolutions.com&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Ajournal&rft.genre=article&rft.atitle=ProxECAT%3A+Proxy+External+Controls+Association+Test.+A+new+case-control+gene+region+association+test+using+allele+frequencies+from+public+controls&rft.jtitle=PLoS+genetics&rft.au=Hendricks%2C+Audrey&rft.au=Billups%2C+Stephen&rft.au=Pike%2C+Hamish&rft.au=Farooqi%2C+I&rft.date=2018-10-01&rft.pub=Public+Library+of+Science&rft.eissn=1553-7404&rft.volume=14&rft.issue=10&rft_id=info:doi/10.1371%2Fjournal.pgen.1007591&rft.externalDocID=2251015221
thumbnail_l http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/lc.gif&issn=1553-7404&client=summon
thumbnail_m http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/mc.gif&issn=1553-7404&client=summon
thumbnail_s http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/sc.gif&issn=1553-7404&client=summon