A real-world pharmacovigilance assessment and literature review of lymphoma development in lipodystrophy

Metreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-tr...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Veröffentlicht in:Frontiers in endocrinology (Lausanne) Jg. 16; S. 1582715
Hauptverfasser: Brown, Rebecca J., Araujo-Vilar, David, Walkovich, Kelly J., Barbarosie, Alexandru, Magee, David A., Akinci, Baris, Oral, Elif A.
Format: Journal Article
Sprache:Englisch
Veröffentlicht: Switzerland Frontiers Media S.A 21.05.2025
Schlagworte:
ISSN:1664-2392, 1664-2392
Online-Zugang:Volltext
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!
Abstract Metreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-treated patients with acquired generalized lipodystrophy (AGL) suggested a possible relationship between metreleptin and lymphoma development. To further investigate this, we performed a real-world pharmacovigilance assessment and literature review to identify lymphomas in patients with lipodystrophy and congenital leptin deficiency (CLD) who were either metreleptin-naïve, or who had previously received/were receiving metreleptin at the time of lymphoma diagnosis. Cases were identified from PubMed, Embase and the Cochrane Library (from database inception through to November 22, 2024), and through review of 11 years post-marketing data from the global safety database (GSD) of the marketing authorization holder for metreleptin. The final analysis set comprised 17 lymphomas in 16 patients reported in 11 published articles and one GSD case report. Twelve lymphomas were recorded in 12 metreleptin-naïve patients - these comprised six T-cell lymphomas (one each in six patients with AGL), three B-cell lymphomas (in two patients with familial partial lipodystrophy and one patient with AGL), and three Hodgkin lymphomas (separately reported in one patient each with generalized lipodystrophy, juvenile-onset dermatomyositis-associated lipodystrophy, and CLD). Five lymphomas were identified in four metreleptin-treated patients, three of whom (all with AGL and T-cell lymphomas) were reported in previously published studies. The remaining metreleptin-treated patient (from the GSD) had generalized lipodystrophy-associated atypical progeroid syndrome and developed a B-cell lymphoma and brain lymphoma following solid organ transplantation and immunosuppressant therapy. All nine T-cell lymphomas occurred in patients with AGL, and additional autoimmune and/or inflammatory disorders were commonly reported in these patients. While a contributory role for metreleptin in lymphoma development in patients with lipodystrophy cannot be excluded, our analysis suggests that lymphoma development may be associated with underlying pathophysiology that also leads to lipodystrophy rather than the pharmacological actions of metreleptin. Our findings support the view that, in some instances, immunoproliferative disorders of T-cells may contribute to syndromes involving autoimmune processes, including AGL.
AbstractList Metreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-treated patients with acquired generalized lipodystrophy (AGL) suggested a possible relationship between metreleptin and lymphoma development. To further investigate this, we performed a real-world pharmacovigilance assessment and literature review to identify lymphomas in patients with lipodystrophy and congenital leptin deficiency (CLD) who were either metreleptin-naïve, or who had previously received/were receiving metreleptin at the time of lymphoma diagnosis.IntroductionMetreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-treated patients with acquired generalized lipodystrophy (AGL) suggested a possible relationship between metreleptin and lymphoma development. To further investigate this, we performed a real-world pharmacovigilance assessment and literature review to identify lymphomas in patients with lipodystrophy and congenital leptin deficiency (CLD) who were either metreleptin-naïve, or who had previously received/were receiving metreleptin at the time of lymphoma diagnosis.Cases were identified from PubMed, Embase and the Cochrane Library (from database inception through to November 22, 2024), and through review of 11 years post-marketing data from the global safety database (GSD) of the marketing authorization holder for metreleptin.MethodsCases were identified from PubMed, Embase and the Cochrane Library (from database inception through to November 22, 2024), and through review of 11 years post-marketing data from the global safety database (GSD) of the marketing authorization holder for metreleptin.The final analysis set comprised 17 lymphomas in 16 patients reported in 11 published articles and one GSD case report. Twelve lymphomas were recorded in 12 metreleptin-naïve patients - these comprised six T-cell lymphomas (one each in six patients with AGL), three B-cell lymphomas (in two patients with familial partial lipodystrophy and one patient with AGL), and three Hodgkin lymphomas (separately reported in one patient each with generalized lipodystrophy, juvenile-onset dermatomyositis-associated lipodystrophy, and CLD). Five lymphomas were identified in four metreleptin-treated patients, three of whom (all with AGL and T-cell lymphomas) were reported in previously published studies. The remaining metreleptin-treated patient (from the GSD) had generalized lipodystrophy-associated atypical progeroid syndrome and developed a B-cell lymphoma and brain lymphoma following solid organ transplantation and immunosuppressant therapy. All nine T-cell lymphomas occurred in patients with AGL, and additional autoimmune and/or inflammatory disorders were commonly reported in these patients.ResultsThe final analysis set comprised 17 lymphomas in 16 patients reported in 11 published articles and one GSD case report. Twelve lymphomas were recorded in 12 metreleptin-naïve patients - these comprised six T-cell lymphomas (one each in six patients with AGL), three B-cell lymphomas (in two patients with familial partial lipodystrophy and one patient with AGL), and three Hodgkin lymphomas (separately reported in one patient each with generalized lipodystrophy, juvenile-onset dermatomyositis-associated lipodystrophy, and CLD). Five lymphomas were identified in four metreleptin-treated patients, three of whom (all with AGL and T-cell lymphomas) were reported in previously published studies. The remaining metreleptin-treated patient (from the GSD) had generalized lipodystrophy-associated atypical progeroid syndrome and developed a B-cell lymphoma and brain lymphoma following solid organ transplantation and immunosuppressant therapy. All nine T-cell lymphomas occurred in patients with AGL, and additional autoimmune and/or inflammatory disorders were commonly reported in these patients.While a contributory role for metreleptin in lymphoma development in patients with lipodystrophy cannot be excluded, our analysis suggests that lymphoma development may be associated with underlying pathophysiology that also leads to lipodystrophy rather than the pharmacological actions of metreleptin. Our findings support the view that, in some instances, immunoproliferative disorders of T-cells may contribute to syndromes involving autoimmune processes, including AGL.DiscussionWhile a contributory role for metreleptin in lymphoma development in patients with lipodystrophy cannot be excluded, our analysis suggests that lymphoma development may be associated with underlying pathophysiology that also leads to lipodystrophy rather than the pharmacological actions of metreleptin. Our findings support the view that, in some instances, immunoproliferative disorders of T-cells may contribute to syndromes involving autoimmune processes, including AGL.
IntroductionMetreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-treated patients with acquired generalized lipodystrophy (AGL) suggested a possible relationship between metreleptin and lymphoma development. To further investigate this, we performed a real-world pharmacovigilance assessment and literature review to identify lymphomas in patients with lipodystrophy and congenital leptin deficiency (CLD) who were either metreleptin-naïve, or who had previously received/were receiving metreleptin at the time of lymphoma diagnosis.MethodsCases were identified from PubMed, Embase and the Cochrane Library (from database inception through to November 22, 2024), and through review of 11 years post-marketing data from the global safety database (GSD) of the marketing authorization holder for metreleptin.ResultsThe final analysis set comprised 17 lymphomas in 16 patients reported in 11 published articles and one GSD case report. Twelve lymphomas were recorded in 12 metreleptin-naïve patients — these comprised six T-cell lymphomas (one each in six patients with AGL), three B-cell lymphomas (in two patients with familial partial lipodystrophy and one patient with AGL), and three Hodgkin lymphomas (separately reported in one patient each with generalized lipodystrophy, juvenile-onset dermatomyositis-associated lipodystrophy, and CLD). Five lymphomas were identified in four metreleptin-treated patients, three of whom (all with AGL and T-cell lymphomas) were reported in previously published studies. The remaining metreleptin-treated patient (from the GSD) had generalized lipodystrophy-associated atypical progeroid syndrome and developed a B-cell lymphoma and brain lymphoma following solid organ transplantation and immunosuppressant therapy. All nine T-cell lymphomas occurred in patients with AGL, and additional autoimmune and/or inflammatory disorders were commonly reported in these patients.DiscussionWhile a contributory role for metreleptin in lymphoma development in patients with lipodystrophy cannot be excluded, our analysis suggests that lymphoma development may be associated with underlying pathophysiology that also leads to lipodystrophy rather than the pharmacological actions of metreleptin. Our findings support the view that, in some instances, immunoproliferative disorders of T-cells may contribute to syndromes involving autoimmune processes, including AGL.
Metreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in lipodystrophy, a rare disease characterized by adipose tissue deficiency. Previously, identification of T-cell lymphomas in three metreleptin-treated patients with acquired generalized lipodystrophy (AGL) suggested a possible relationship between metreleptin and lymphoma development. To further investigate this, we performed a real-world pharmacovigilance assessment and literature review to identify lymphomas in patients with lipodystrophy and congenital leptin deficiency (CLD) who were either metreleptin-naïve, or who had previously received/were receiving metreleptin at the time of lymphoma diagnosis. Cases were identified from PubMed, Embase and the Cochrane Library (from database inception through to November 22, 2024), and through review of 11 years post-marketing data from the global safety database (GSD) of the marketing authorization holder for metreleptin. The final analysis set comprised 17 lymphomas in 16 patients reported in 11 published articles and one GSD case report. Twelve lymphomas were recorded in 12 metreleptin-naïve patients - these comprised six T-cell lymphomas (one each in six patients with AGL), three B-cell lymphomas (in two patients with familial partial lipodystrophy and one patient with AGL), and three Hodgkin lymphomas (separately reported in one patient each with generalized lipodystrophy, juvenile-onset dermatomyositis-associated lipodystrophy, and CLD). Five lymphomas were identified in four metreleptin-treated patients, three of whom (all with AGL and T-cell lymphomas) were reported in previously published studies. The remaining metreleptin-treated patient (from the GSD) had generalized lipodystrophy-associated atypical progeroid syndrome and developed a B-cell lymphoma and brain lymphoma following solid organ transplantation and immunosuppressant therapy. All nine T-cell lymphomas occurred in patients with AGL, and additional autoimmune and/or inflammatory disorders were commonly reported in these patients. While a contributory role for metreleptin in lymphoma development in patients with lipodystrophy cannot be excluded, our analysis suggests that lymphoma development may be associated with underlying pathophysiology that also leads to lipodystrophy rather than the pharmacological actions of metreleptin. Our findings support the view that, in some instances, immunoproliferative disorders of T-cells may contribute to syndromes involving autoimmune processes, including AGL.
Author Walkovich, Kelly J.
Oral, Elif A.
Akinci, Baris
Brown, Rebecca J.
Araujo-Vilar, David
Magee, David A.
Barbarosie, Alexandru
AuthorAffiliation 3 Division of Pediatric Hematology/Oncology, Department of Pediatrics, University of Michigan , Ann Arbor, MI , United States
6 Metabolism, Endocrinology and Diabetes Division, Department of Internal Medicine, Caswell Diabetes Institute, North Campus Research Complex, University of Michigan , Ann Arbor, MI , United States
2 UETeM−Molecular Pathology of Rare Diseases Group, Center for Research in Molecular Medicine and Chronic Diseases (CIMUS), School of Medicine and Dentistry, University of Santiago de Compostela , Santiago de Compostela , Spain
5 Izmir Biomedicine and Genome Center & Dokuz Eylul University Technopark (DEPARK), Dokuz Eylul University Health Campus , Izmir , Türkiye
4 Chiesi Global Rare Diseases , Dublin , Ireland
1 Diabetes, Endocrinology, and Obesity Branch, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health , Bethesda, MD , United States
AuthorAffiliation_xml – name: 2 UETeM−Molecular Pathology of Rare Diseases Group, Center for Research in Molecular Medicine and Chronic Diseases (CIMUS), School of Medicine and Dentistry, University of Santiago de Compostela , Santiago de Compostela , Spain
– name: 6 Metabolism, Endocrinology and Diabetes Division, Department of Internal Medicine, Caswell Diabetes Institute, North Campus Research Complex, University of Michigan , Ann Arbor, MI , United States
– name: 4 Chiesi Global Rare Diseases , Dublin , Ireland
– name: 3 Division of Pediatric Hematology/Oncology, Department of Pediatrics, University of Michigan , Ann Arbor, MI , United States
– name: 5 Izmir Biomedicine and Genome Center & Dokuz Eylul University Technopark (DEPARK), Dokuz Eylul University Health Campus , Izmir , Türkiye
– name: 1 Diabetes, Endocrinology, and Obesity Branch, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health , Bethesda, MD , United States
Author_xml – sequence: 1
  givenname: Rebecca J.
  surname: Brown
  fullname: Brown, Rebecca J.
– sequence: 2
  givenname: David
  surname: Araujo-Vilar
  fullname: Araujo-Vilar, David
– sequence: 3
  givenname: Kelly J.
  surname: Walkovich
  fullname: Walkovich, Kelly J.
– sequence: 4
  givenname: Alexandru
  surname: Barbarosie
  fullname: Barbarosie, Alexandru
– sequence: 5
  givenname: David A.
  surname: Magee
  fullname: Magee, David A.
– sequence: 6
  givenname: Baris
  surname: Akinci
  fullname: Akinci, Baris
– sequence: 7
  givenname: Elif A.
  surname: Oral
  fullname: Oral, Elif A.
BackLink https://www.ncbi.nlm.nih.gov/pubmed/40469440$$D View this record in MEDLINE/PubMed
BookMark eNpVkstu3CAUhlGUqLk0L5BF5WU3nnC1zaqKol4iReqmWSMMhzERNi54Jpq3L5mZRgmIi-DjP3D4L9HpFCdA6IbgFWOdvHUw2biimIoVER1tiThBF6RpeE2ZpKfv5ufoOudnXArHRMruEzrnmDeSc3yBhrsqgQ71S0zBVvOg06hN3Pq1D3oyUOmcIecRpqXSk62CXyDpZZOgHNt6eKmiq8JunIc46srCFkKc97SfCjxHu8tLivOw-4zOnA4Zro_jFXr68f3P_a_68ffPh_u7x9pwSpe677htWkb7xpnGUNFzKYwrleOWGstMA5xzVpCOccMdA9a5XrStxFCaZFfo4aBro35Wc_KjTjsVtVf7hZjWSqfFmwCq6XRvLO9boXveWiddzzpeMikkcVjqovXtoDVv-hGsKe9KOnwQ_bgz-UGt41YRShgT-9t8PSqk-HcDeVGjzwZCSS7ETVaMEiG7pvQF_fI-2FuU_39VAHoATIo5J3BvCMHq1RNq7wn16gl19AT7B1x1rRg
Cites_doi 10.2147/DMSO.S130810
10.2337/db21-1086
10.3109/10428194.2015.1040015
10.1111/dom.15882
10.3389/fendo.2023.1250203
10.1056/NEJMra1702693
10.1210/jcemcr/luae069
10.1007/s12020-019-01862-8
10.1371/journal.pone.0199052
10.1158/1055-9965.EPI-06-1069
10.1056/NEJMra025261
10.1172/JCI15693
10.1158/1055-9965.EPI-06-0300
10.3389/fimmu.2018.02142
10.1210/jc.2017-02078
10.3389/fimmu.2020.622468
10.1016/j.imlet.2023.08.007
10.1038/29795
10.1007/s12020-018-1589-1
10.1210/jc.2016-2466
10.1038/ng0398-213
10.1016/j.nmd.2018.06.011
10.1016/j.ecl.2017.01.012
10.1210/jendso/bvac150.065
10.1038/bjc.2015.94
10.1210/jcem.84.10.5999
10.1210/jc.2018-02730
10.1007/s12020-014-0450-4
10.1210/jc.2011-1159
10.1007/s40265-013-0074-7
10.1080/17446651.2020.1735360
10.1038/s42255-019-0095-y
10.1001/archinte.1978.03630330097036
10.1016/j.semcancer.2013.12.001
10.1210/jendso/bvaa046.1059
10.1210/clinem/dgae149
10.1186/s40842-019-0076-9
10.1210/jc.2005-1220
10.1016/j.eclinm.2022.101674
10.1038/43185
10.4158/ACCR-2019-0366
10.2169/internalmedicine.53.1713
10.3390/medsci9010005
10.1002/art.21675
10.1097/00005792-200303000-00007
10.1210/jcem.87.5.8624
10.1111/j.1365-2796.2008.02029.x
10.1111/ijd.12185
10.1111/j.1365-4632.2006.02888.x
10.1097/01.md.0000111061.69212.59
10.1007/978-1-62703-170-7_2
10.1096/fsb2fasebj.12.1.57
10.1056/NEJMoa012437
10.1056/NEJMoa2204041
10.1056/NEJM199909163411204
ContentType Journal Article
Copyright Copyright © 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral.
Copyright © 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral
Copyright_xml – notice: Copyright © 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral.
– notice: Copyright © 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral
DBID AAYXX
CITATION
CGR
CUY
CVF
ECM
EIF
NPM
7X8
5PM
DOA
DOI 10.3389/fendo.2025.1582715
DatabaseName CrossRef
Medline
MEDLINE
MEDLINE (Ovid)
MEDLINE
MEDLINE
PubMed
MEDLINE - Academic
PubMed Central (Full Participant titles)
DOAJ Directory of Open Access Journals
DatabaseTitle CrossRef
MEDLINE
Medline Complete
MEDLINE with Full Text
PubMed
MEDLINE (Ovid)
MEDLINE - Academic
DatabaseTitleList MEDLINE - Academic

MEDLINE
Database_xml – sequence: 1
  dbid: DOA
  name: DOAJ Directory of Open Access Journals
  url: https://www.doaj.org/
  sourceTypes: Open Website
– sequence: 2
  dbid: NPM
  name: PubMed
  url: http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?db=PubMed
  sourceTypes: Index Database
– sequence: 3
  dbid: 7X8
  name: MEDLINE - Academic
  url: https://search.proquest.com/medline
  sourceTypes: Aggregation Database
DeliveryMethod fulltext_linktorsrc
Discipline Medicine
EISSN 1664-2392
ExternalDocumentID oai_doaj_org_article_68abcd4b75ab47df9fb384715591f09a
PMC12133509
40469440
10_3389_fendo_2025_1582715
Genre Journal Article
Review
GroupedDBID 53G
5VS
9T4
AAFWJ
AAKDD
AAYXX
ACGFO
ACGFS
ADBBV
ADRAZ
AFPKN
ALMA_UNASSIGNED_HOLDINGS
AOIJS
BAWUL
BCNDV
CITATION
DIK
EMOBN
GROUPED_DOAJ
GX1
HYE
KQ8
M~E
OK1
PGMZT
RPM
ACXDI
CGR
CUY
CVF
ECM
EIF
IPNFZ
M48
NPM
RIG
7X8
5PM
ID FETCH-LOGICAL-c422t-b84d6732b6fc6c25b495cfcfc4072cd3c6e4443673834c4f3e38fb57790e79093
IEDL.DBID DOA
ISICitedReferencesCount 0
ISICitedReferencesURI http://www.webofscience.com/api/gateway?GWVersion=2&SrcApp=Summon&SrcAuth=ProQuest&DestLinkType=CitingArticles&DestApp=WOS_CPL&KeyUT=001503827400001&url=https%3A%2F%2Fcvtisr.summon.serialssolutions.com%2F%23%21%2Fsearch%3Fho%3Df%26include.ft.matches%3Dt%26l%3Dnull%26q%3D
ISSN 1664-2392
IngestDate Fri Oct 03 12:43:40 EDT 2025
Thu Aug 21 18:25:41 EDT 2025
Fri Sep 05 15:55:25 EDT 2025
Thu Jun 19 02:16:00 EDT 2025
Sat Nov 29 07:51:21 EST 2025
IsDoiOpenAccess true
IsOpenAccess true
IsPeerReviewed true
IsScholarly true
Keywords acquired generalized lipodystrophy
autoimmunity
B cell lymphoma
lymphoma
metreleptin
pharmacovigilance
T-cell lymphoma
lipodystrophy
Language English
License Copyright © 2025 Brown, Araujo-Vilar, Walkovich, Barbarosie, Magee, Akinci and Oral.
This is an open-access article distributed under the terms of the Creative Commons Attribution License (CC BY). The use, distribution or reproduction in other forums is permitted, provided the original author(s) and the copyright owner(s) are credited and that the original publication in this journal is cited, in accordance with accepted academic practice. No use, distribution or reproduction is permitted which does not comply with these terms.
LinkModel DirectLink
MergedId FETCHMERGED-LOGICAL-c422t-b84d6732b6fc6c25b495cfcfc4072cd3c6e4443673834c4f3e38fb57790e79093
Notes ObjectType-Article-1
SourceType-Scholarly Journals-1
ObjectType-Feature-2
ObjectType-Review-3
content type line 23
Edited by: Tao Zhang, West China Hospital, China
Brigitte Delemer, Université de Reims Champagne-Ardenne, France
Reviewed by: Elif Ozsu, Ankara University Medical School, Türkiye
OpenAccessLink https://doaj.org/article/68abcd4b75ab47df9fb384715591f09a
PMID 40469440
PQID 3215986215
PQPubID 23479
ParticipantIDs doaj_primary_oai_doaj_org_article_68abcd4b75ab47df9fb384715591f09a
pubmedcentral_primary_oai_pubmedcentral_nih_gov_12133509
proquest_miscellaneous_3215986215
pubmed_primary_40469440
crossref_primary_10_3389_fendo_2025_1582715
PublicationCentury 2000
PublicationDate 2025-05-21
PublicationDateYYYYMMDD 2025-05-21
PublicationDate_xml – month: 05
  year: 2025
  text: 2025-05-21
  day: 21
PublicationDecade 2020
PublicationPlace Switzerland
PublicationPlace_xml – name: Switzerland
PublicationTitle Frontiers in endocrinology (Lausanne)
PublicationTitleAlternate Front Endocrinol (Lausanne)
PublicationYear 2025
Publisher Frontiers Media S.A
Publisher_xml – name: Frontiers Media S.A
References Garg (B3) 2011; 96
B22
B23
Wang (B36) 2013
Corvillo (B5) 2023; 72
B24
B25
Chou (B21) 2013; 73
B26
B27
Kolijn (B49) 2023; 263
Yiannias (B55) 2006; 45
Lima (B48) 2018; 13
Oral (B18) 2002; 346
Kiernan (B45) 2020; 11
Oral (B46) 2006; 91
Misra (B7) 2003; 82
Hoff (B42) 2024; 2
B31
Brown (B1) 2016; 101
Friedman (B9) 2019; 1
Montague (B15) 1997; 387
Baecklund (B37) 2006; 54
Garg (B2) 2004; 350
von Schnurbein (B17) 2024; 109
Ozata (B47) 1999; 84
Thandra (B53) 2021; 9
Smedby (B39) 2006; 15
Funcke (B29) 2023; 388
Lightbourne (B6) 2017; 46
Strobel (B16) 1998; 18
Oral (B20) 2019; 64
Araujo-Vilar (B32) 2015; 49
de Andrade (B59) 2020; 6
Corvillo (B40) 2018; 9
Baecklund (B41) 2014; 24
Hall (B62) 1978; 138
Torchen (B64); 4
Brown (B19) 2018; 60
Haque (B10) 2002; 87
Fernandez-Pombo (B13) 2024; 26
Farooqi (B14) 1999; 341
Akinci (B11) 2019; 104
Rego de Figueiredo (B61) 2018; 28
Foss-Freitas (B54) 2020; 15
Smith (B35) 2015; 112
Aslam (B56) 2015; 54
Chiquette (B34) 2017; 10
Torchen (B63); 6
Krishnan (B51) 2007; 16
Loffreda (B43) 1998; 12
Akinci (B4) 2000
Dierickx (B50) 2018; 378
Smedby (B38) 2008; 264
Misra (B8) 2004; 83
Brown (B30) 2016; 57
Fernandez-Pombo (B12) 2023; 14
Lord (B44) 1998; 394
Farooqi (B28) 2002; 110
Hussain (B33) 2018; 103
Esfandiari (B57) 2019; 5
Ebihara (B58)
Donzel (B52) 2022; 54
Iwanishi (B60) 2014; 53
References_xml – volume: 10
  year: 2017
  ident: B34
  article-title: Estimating the prevalence of generalized and partial lipodystrophy: findings and challenges
  publication-title: Diabetes Metab Syndr Obes
  doi: 10.2147/DMSO.S130810
– volume: 72
  start-page: 71
  year: 2023
  ident: B5
  article-title: Characterization and clinical association of autoantibodies against perilipin 1 in patients with acquired generalized lipodystrophy
  publication-title: Diabetes
  doi: 10.2337/db21-1086
– volume: 57
  start-page: 45
  year: 2016
  ident: B30
  article-title: Lymphoma in acquired generalized lipodystrophy
  publication-title: Leuk Lymphoma
  doi: 10.3109/10428194.2015.1040015
– volume: 26
  year: 2024
  ident: B13
  article-title: A cohort analysis of familial partial lipodystrophy from two mediterranean countries
  publication-title: Diabetes Obes Metab
  doi: 10.1111/dom.15882
– volume: 14
  year: 2023
  ident: B12
  article-title: Natural history and comorbidities of generalized and partial lipodystrophy syndromes in Spain
  publication-title: Front Endocrinol (Lausanne)
  doi: 10.3389/fendo.2023.1250203
– volume: 378
  year: 2018
  ident: B50
  article-title: Post-transplantation lymphoproliferative disorders in adults
  publication-title: N Engl J Med
  doi: 10.1056/NEJMra1702693
– volume: 2
  year: 2024
  ident: B42
  article-title: A novel subtype of acquired generalized lipodystrophy associated with subcutaneous panniculitis-like T-cell lymphoma
  publication-title: JCEM Case Rep
  doi: 10.1210/jcemcr/luae069
– ident: B25
– volume: 64
  year: 2019
  ident: B20
  article-title: Long-term effectiveness and safety of metreleptin in the treatment of patients with partial lipodystrophy
  publication-title: Endocrine
  doi: 10.1007/s12020-019-01862-8
– volume: 13
  year: 2018
  ident: B48
  article-title: Causes of death in patients with Berardinelli-Seip congenital generalized lipodystrophy
  publication-title: PloS One
  doi: 10.1371/journal.pone.0199052
– volume: 16
  year: 2007
  ident: B51
  article-title: Non-hodgkin lymphoma secondary to cancer chemotherapy
  publication-title: Cancer Epidemiol Biomarkers Prev
  doi: 10.1158/1055-9965.EPI-06-1069
– ident: B31
– volume: 350
  year: 2004
  ident: B2
  article-title: Acquired and inherited lipodystrophies
  publication-title: N Engl J Med
  doi: 10.1056/NEJMra025261
– volume: 110
  year: 2002
  ident: B28
  article-title: Beneficial effects of leptin on obesity, T cell hyporesponsiveness, and neuroendocrine/metabolic dysfunction of human congenital leptin deficiency
  publication-title: J Clin Invest
  doi: 10.1172/JCI15693
– volume: 15
  year: 2006
  ident: B39
  article-title: Malignant lymphomas in autoimmunity and inflammation: A review of risks, risk factors, and lymphoma characteristics
  publication-title: Cancer Epidemiol Biomarkers Prev
  doi: 10.1158/1055-9965.EPI-06-0300
– volume: 9
  year: 2018
  ident: B40
  article-title: Autoantibodies against perilipin 1 as a cause of acquired generalized lipodystrophy
  publication-title: Front Immunol
  doi: 10.3389/fimmu.2018.02142
– volume: 103
  year: 2018
  ident: B33
  article-title: A novel generalized lipodystrophy-associated progeroid syndrome due to recurrent heterozygous LMNA P.T10i mutation
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jc.2017-02078
– volume: 11
  year: 2020
  ident: B45
  article-title: The role of the adipokine leptin in immune cell function in health and disease
  publication-title: Front Immunol
  doi: 10.3389/fimmu.2020.622468
– volume: 263
  start-page: 46
  year: 2023
  ident: B49
  article-title: Immune dysregulation as a leading principle for lymphoma development in diverse immunological backgrounds
  publication-title: Immunol Lett
  doi: 10.1016/j.imlet.2023.08.007
– volume: 394
  start-page: 897
  year: 1998
  ident: B44
  article-title: Leptin modulates the T-cell immune response and reverses starvation-induced immunosuppression
  publication-title: Nature
  doi: 10.1038/29795
– volume: 60
  year: 2018
  ident: B19
  article-title: Long-term effectiveness and safety of metreleptin in the treatment of patients with generalized lipodystrophy
  publication-title: Endocrine
  doi: 10.1007/s12020-018-1589-1
– volume: 101
  year: 2016
  ident: B1
  article-title: The diagnosis and management of lipodystrophy syndromes: A multi-society practice guideline
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jc.2016-2466
– volume: 18
  year: 1998
  ident: B16
  article-title: A leptin missense mutation associated with hypogonadism and morbid obesity
  publication-title: . Nat Genet
  doi: 10.1038/ng0398-213
– volume: 28
  year: 2018
  ident: B61
  article-title: Juvenile dermatomyositis forty years on: case report
  publication-title: Neuromuscul Disord
  doi: 10.1016/j.nmd.2018.06.011
– volume: 46
  year: 2017
  ident: B6
  article-title: Genetics of lipodystrophy
  publication-title: Endocrinol Metab Clin North Am
  doi: 10.1016/j.ecl.2017.01.012
– volume: 6
  ident: B63
  article-title: Lymphoma in congenital leptin deficiency: comorbidity or adverse effect
  doi: 10.1210/jendso/bvac150.065
– ident: B24
– volume: 112
  year: 2015
  ident: B35
  article-title: Lymphoma incidence, survival and prevalence 2004-2014: sub-type analyses from the UK's Haematological Malignancy research network
  publication-title: Br J Cancer
  doi: 10.1038/bjc.2015.94
– volume: 84
  year: 1999
  ident: B47
  article-title: Human leptin deficiency caused by a missense mutation: multiple endocrine defects, decreased sympathetic tone, and immune system dysfunction indicate new targets for leptin action, greater central than peripheral resistance to the effects of leptin, and spontaneous correction of leptin-mediated defects
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jcem.84.10.5999
– volume: 104
  year: 2019
  ident: B11
  article-title: Comorbidities and survival in patients with lipodystrophy: an international chart review study
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jc.2018-02730
– volume: 49
  year: 2015
  ident: B32
  article-title: Recombinant human leptin treatment in genetic lipodystrophic syndromes: the long-term spanish experience
  publication-title: Endocrine
  doi: 10.1007/s12020-014-0450-4
– volume: 96
  year: 2011
  ident: B3
  article-title: Clinical review: lipodystrophies: genetic and acquired body fat disorders
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jc.2011-1159
– volume: 73
  year: 2013
  ident: B21
  article-title: Metreleptin: first global approval
  publication-title: Drugs
  doi: 10.1007/s40265-013-0074-7
– volume: 15
  start-page: 95
  year: 2020
  ident: B54
  article-title: Diagnostic strategies and clinical management of lipodystrophy
  publication-title: Expert Rev Endocrinol Metab
  doi: 10.1080/17446651.2020.1735360
– volume: 1
  year: 2019
  ident: B9
  article-title: Leptin and the endocrine control of energy balance
  publication-title: Nat Metab
  doi: 10.1038/s42255-019-0095-y
– volume: 138
  year: 1978
  ident: B62
  article-title: Generalized lipodystrophy, scleroderma, and hodgkin’s disease
  publication-title: Arch Intern Med
  doi: 10.1001/archinte.1978.03630330097036
– volume: 24
  start-page: 61
  year: 2014
  ident: B41
  article-title: Lymphoma development in patients with autoimmune and inflammatory disorders–what are the driving forces
  publication-title: Semin Cancer Biol
  doi: 10.1016/j.semcancer.2013.12.001
– volume: 4
  ident: B64
  article-title: Congenital leptin deficiency: clinical insights from the first reported US cases
  doi: 10.1210/jendso/bvaa046.1059
– volume-title: Lipodystrophy syndromes: presentation and treatment
  year: 2000
  ident: B4
– volume: 109
  year: 2024
  ident: B17
  article-title: Classification of congenital leptin deficiency
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/clinem/dgae149
– ident: B27
– volume: 5
  year: 2019
  ident: B57
  article-title: Diagnosis of acquired generalized lipodystrophy in a single patient with T-cell lymphoma and no exposure to metreleptin
  publication-title: Clin Diabetes Endocrinol
  doi: 10.1186/s40842-019-0076-9
– ident: B23
– volume: 91
  year: 2006
  ident: B46
  article-title: Leptin replacement therapy modulates circulating lymphocyte subsets and cytokine responsiveness in severe lipodystrophy
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jc.2005-1220
– volume: 54
  year: 2022
  ident: B52
  article-title: Lymphomas associated with epstein-barr virus infection in 2020: results from a large, unselected case series in France
  publication-title: EClinicalMedicine
  doi: 10.1016/j.eclinm.2022.101674
– volume: 387
  year: 1997
  ident: B15
  article-title: Congenital leptin deficiency is associated with severe early-onset obesity in humans
  publication-title: Nature
  doi: 10.1038/43185
– volume: 6
  year: 2020
  ident: B59
  article-title: Unusual presentations of LMNA-associated lipodystrophy with complex phenotypes and generalized fat loss: when the genetic diagnosis uncovers novel features
  publication-title: AACE Clin Case Rep
  doi: 10.4158/ACCR-2019-0366
– volume: 53
  year: 2014
  ident: B60
  article-title: Primary intestinal follicular lymphoma and premature atherosclerosis in a Japanese diabetic patient with atypical familial partial lipodystrophy
  publication-title: Intern Med
  doi: 10.2169/internalmedicine.53.1713
– volume: 9
  start-page: 20210130
  year: 2021
  ident: B53
  article-title: Epidemiology of non-hodgkin’s lymphoma
  publication-title: Med Sci (Basel)
  doi: 10.3390/medsci9010005
– volume: 54
  start-page: 692
  year: 2006
  ident: B37
  article-title: Association of chronic inflammation, not its treatment, with increased lymphoma risk in rheumatoid arthritis
  publication-title: Arthritis Rheum
  doi: 10.1002/art.21675
– volume: 82
  year: 2003
  ident: B7
  article-title: Clinical features and metabolic derangements in acquired generalized lipodystrophy: case reports and review of the literature
  publication-title: Med (Baltimore)
  doi: 10.1097/00005792-200303000-00007
– volume: 87
  start-page: 2395
  year: 2002
  ident: B10
  article-title: Serum adiponectin and leptin levels in patients with lipodystrophies
  publication-title: J Clin Endocrinol Metab
  doi: 10.1210/jcem.87.5.8624
– volume: 264
  year: 2008
  ident: B38
  article-title: Autoimmune and inflammatory disorders and risk of Malignant lymphomas–an update
  publication-title: J Intern Med
  doi: 10.1111/j.1365-2796.2008.02029.x
– volume-title: Endocrine Reviews
  ident: B58
– volume: 54
  year: 2015
  ident: B56
  article-title: Acquired generalized lipodystrophy associated with peripheral T cell lymphoma with cutaneous infiltration
  publication-title: Int J Dermatol
  doi: 10.1111/ijd.12185
– ident: B26
– volume: 45
  year: 2006
  ident: B55
  article-title: Peripheral T-cell lymphoma presenting as lipoatrophy and nodules
  publication-title: Int J Dermatol
  doi: 10.1111/j.1365-4632.2006.02888.x
– volume: 83
  start-page: 18
  year: 2004
  ident: B8
  article-title: Clinical features and metabolic and autoimmune derangements in acquired partial lipodystrophy: report of 35 cases and review of the literature
  publication-title: Med (Baltimore)
  doi: 10.1097/01.md.0000111061.69212.59
– start-page: 25
  volume-title: T-cell lymphomas
  year: 2013
  ident: B36
  article-title: Epidemiology and prognosis of T-cell lymphoma
  doi: 10.1007/978-1-62703-170-7_2
– ident: B22
– volume: 12
  start-page: 57
  year: 1998
  ident: B43
  article-title: Leptin regulates proinflammatory immune responses
  publication-title: FASEB J
  doi: 10.1096/fsb2fasebj.12.1.57
– volume: 346
  year: 2002
  ident: B18
  article-title: Leptin-replacement therapy for lipodystrophy
  publication-title: N Engl J Med
  doi: 10.1056/NEJMoa012437
– volume: 388
  year: 2023
  ident: B29
  article-title: Rare antagonistic leptin variants and severe, early-onset obesity
  publication-title: N Engl J Med
  doi: 10.1056/NEJMoa2204041
– volume: 341
  year: 1999
  ident: B14
  article-title: Effects of recombinant leptin therapy in a child with congenital leptin deficiency
  publication-title: N Engl J Med
  doi: 10.1056/NEJM199909163411204
SSID ssj0000401998
Score 2.3690157
SecondaryResourceType review_article
Snippet Metreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin deficiency in...
IntroductionMetreleptin is a form of leptin replacement therapy used with diet and lifestyle modifications to treat the metabolic complications of leptin...
SourceID doaj
pubmedcentral
proquest
pubmed
crossref
SourceType Open Website
Open Access Repository
Aggregation Database
Index Database
StartPage 1582715
SubjectTerms acquired generalized lipodystrophy
Adult
autoimmunity
B cell lymphoma
Endocrinology
Female
Humans
Leptin - adverse effects
Leptin - analogs & derivatives
Leptin - therapeutic use
lipodystrophy
Lipodystrophy - complications
Lipodystrophy - drug therapy
lymphoma
Lymphoma - chemically induced
Lymphoma - epidemiology
Male
Middle Aged
Pharmacovigilance
T-cell lymphoma
Title A real-world pharmacovigilance assessment and literature review of lymphoma development in lipodystrophy
URI https://www.ncbi.nlm.nih.gov/pubmed/40469440
https://www.proquest.com/docview/3215986215
https://pubmed.ncbi.nlm.nih.gov/PMC12133509
https://doaj.org/article/68abcd4b75ab47df9fb384715591f09a
Volume 16
WOSCitedRecordID wos001503827400001&url=https%3A%2F%2Fcvtisr.summon.serialssolutions.com%2F%23%21%2Fsearch%3Fho%3Df%26include.ft.matches%3Dt%26l%3Dnull%26q%3D
hasFullText 1
inHoldings 1
isFullTextHit
isPrint
journalDatabaseRights – providerCode: PRVAON
  databaseName: DOAJ Directory of Open Access Journals
  customDbUrl:
  eissn: 1664-2392
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0000401998
  issn: 1664-2392
  databaseCode: DOA
  dateStart: 20100101
  isFulltext: true
  titleUrlDefault: https://www.doaj.org/
  providerName: Directory of Open Access Journals
– providerCode: PRVHPJ
  databaseName: ROAD: Directory of Open Access Scholarly Resources
  customDbUrl:
  eissn: 1664-2392
  dateEnd: 99991231
  omitProxy: false
  ssIdentifier: ssj0000401998
  issn: 1664-2392
  databaseCode: M~E
  dateStart: 20100101
  isFulltext: true
  titleUrlDefault: https://road.issn.org
  providerName: ISSN International Centre
link http://cvtisr.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwrV1Na9wwEB3SUEovoW3aZvsRVOituNnVh20d05DQS0IOLexN6LMxbO1ldxPIJb-9M7Kz2S2FXIqxD7ZAYp4tvWdJbwA-ezfmqAJ44UXpCqm0Kizy5iIpr-XEISOvQk42UV1c1NOpvtxI9UVrwnp74D5wR2VtnQ_SVco6WYWkkxPUoyITnqSxztQIWc-GmMp9MMoGFBL9LhlUYfooxTbQZj-uvk5UzSvKg7sxEmXD_n-xzL8XS26MPmcvYG-gjey4b-5L2IntK3h2PkyM78PVMUP2NyuyASqbD37UN82vZkawMrs24GS2DWy2NlNm_d4V1iU2u0Vku9-WhYeFRKxpsfC8C7fL1aJDSF7Dz7PTHyffiyGJQuEl56vC1TKUleC0qaf0XDlURD7hQc5oPghfRimloOSfQnqZRBR1copsCCOeWryB3bZr4wEwVDsW5YqMKlipObdOI91MpbWBixjKEXy5D6iZ914ZBjUGhd_k8BsKvxnCP4JvFPN1SfK5zjcQfTOgbx5DfwSf7hEz-F3QZIdtY3e9NAK5jEa5RhW97RFcVyXpp4CU4xHUW9hutWX7SdtcZe9tcsATSLLe_Y_Wv4fnFBFajMAnH2B3tbiOH-Gpv1k1y8UhPKmm9WF-r_F6fnf6B-qBAG8
linkProvider Directory of Open Access Journals
openUrl ctx_ver=Z39.88-2004&ctx_enc=info%3Aofi%2Fenc%3AUTF-8&rfr_id=info%3Asid%2Fsummon.serialssolutions.com&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Ajournal&rft.genre=article&rft.atitle=A+real-world+pharmacovigilance+assessment+and+literature+review+of+lymphoma+development+in+lipodystrophy&rft.jtitle=Frontiers+in+endocrinology+%28Lausanne%29&rft.au=Brown%2C+Rebecca+J.&rft.au=Araujo-Vilar%2C+David&rft.au=Walkovich%2C+Kelly+J.&rft.au=Barbarosie%2C+Alexandru&rft.date=2025-05-21&rft.issn=1664-2392&rft.eissn=1664-2392&rft.volume=16&rft_id=info:doi/10.3389%2Ffendo.2025.1582715&rft.externalDBID=n%2Fa&rft.externalDocID=10_3389_fendo_2025_1582715
thumbnail_l http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/lc.gif&issn=1664-2392&client=summon
thumbnail_m http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/mc.gif&issn=1664-2392&client=summon
thumbnail_s http://covers-cdn.summon.serialssolutions.com/index.aspx?isbn=/sc.gif&issn=1664-2392&client=summon