The French compassionate programme of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del CFTR variant

The European Medicines Agency has approved the cystic fibrosis transmembrane conductance regulator (CFTR) modulator combination elexacaftor/tezacaftor/ivacaftor (ETI) for people with cystic fibrosis (CF) carrying at least one F508del variant. The United States Food and Drug Administration (FDA) also...

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Veröffentlicht in:The European respiratory journal Jg. 61; H. 5
Hauptverfasser: Burgel, Pierre-Régis, Sermet-Gaudelus, Isabelle, Durieu, Isabelle, Kanaan, Reem, Macey, Julie, Grenet, Dominique, Porzio, Michele, Coolen-Allou, Nathalie, Chiron, Raphael, Marguet, Christophe, Douvry, Benoit, Dufeu, Nadine, Danner-Boucher, Isabelle, Foucaud, Pierre, Lemonnier, Lydie, Girodon, Emmanuelle, Da Silva, Jennifer, Martin, Clémence, Andrejak, Claire, Priou, Pascaline, Richaud-Thiriez, Bénédicte, Montcouquiol, Sylvie, Remus, Natacha, Fanton, Annlyse, Gachelin, Elsa, Vuillard, Constance, Audousset, Camille, Duthoit, Louise, Bellet-Fraysse, Elisabeth, Languepin, Jeanne, Nove-Josserand, Raphaele, Ohlmann, Camille, Raynaud, Quitterie, Billon, Yves, Tissot, Adrien, Leroy, Sylvie, Aubourg, Frédérique, Burnet, Espérie, Carlier, Nicolas, Fajac, Isabelle, Honoré, Isabelle, Le Bourgeois, Muriel, Le Clainche-Viala, Laurence, Corvol, Harriet, Dehillotte, Clémence, Brinchault, Graziella, Ravoninjatovo, Bruno, Le Bihan, Jean, Ramel, Sophie, Weiss, Laurence, de Miranda, Sandra, Cosson, Laure, Mankikian, Julie, Pouradier, Delphine
Format: Journal Article
Sprache:Englisch
Veröffentlicht: England 01.05.2023
ISSN:1399-3003, 1399-3003
Online-Zugang:Weitere Angaben
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