Caregiver risk preferences for delaying loss of ambulation in Duchenne muscular dystrophy in the United States

Quantify caregiver risk preferences to inform the "value of hope" for Duchenne muscular dystrophy (DMD) therapies affecting time to loss of ambulation (LoA). Caregivers (medical decision-makers) of patients with DMD were surveyed to evaluate their preferences across 2 therapies with identi...

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Bibliographic Details
Published in:	Current medical research and opinion Vol. 41; no. 8; pp. 1499 - 1509
Main Authors:	Shafrin, Jason, Zawadzki, Nadine, Marin, Moises, Audhya, Ivana, Sedita, Lauren E., Kulkarni, Natasha, Klimchak, Alexa C.
Format:	Journal Article
Language:	English
Published:	England 03.08.2025
Subjects:	Adolescent Adult Caregivers - psychology Child Child, Preschool Female Humans Male Middle Aged Muscular Dystrophy, Duchenne - physiopathology Muscular Dystrophy, Duchenne - therapy Time Factors United States Walking United States treatment preferences loss of ambulation value of hope value assessment Duchenne muscular dystrophy
ISSN:	0300-7995, 1473-4877, 1473-4877
Online Access:	Get full text
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