Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy - Sergio Muñoz; Joan Bertolin; Veronica Jimenez; Maria Luisa Jaén; Miquel Garcia; Anna Pujol; Laia Vilà; Victor Sacristan; Elena Barbon; Giuseppe Ronzitti; Jihad El Andari; Warut Tulalamba; et al. (Molecular Metabolism, 2024)