Search Results - "Research & Experimental"
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1
Authors: et al.
Source: Dipalo, L L, Mikkelsen, J G, Gijsbers, R & Carlon, M S 2025, 'Trojan Horse-Like Vehicles for CRISPR-Cas Delivery : Engineering Extracellular Vesicles and Virus-Like Particles for Precision Gene Editing in Cystic Fibrosis', Human Gene Therapy. https://doi.org/10.1089/hum.2024.258
Subject Terms: Cystic Fibrosis, DIRECTED EVOLUTION, Genetic Vectors, VIRAL-INFECTION, Research & Experimental Medicine, MEMBRANE-FUSION, virus-like particles, ENDOSOMAL ESCAPE, Extracellular Vesicles, IMMUNE-RESPONSE, Humans, Animals, Genetics & Heredity, Gene Editing, Science & Technology, HUMAN-CELLS, 1004 Medical Biotechnology, Gene Transfer Techniques, Virion, MURINE LEUKEMIA-VIRUS, 1103 Clinical Sciences, VESICULAR STOMATITIS-VIRUS, Genetic Therapy, ENVELOPE PROTEINS, in vivo CRISPR delivery, LENTIVIRAL VECTOR PRODUCTION, lung-targeted delivery, Biotechnology & Applied Microbiology, Medicine, Research & Experimental, CRISPR-Cas gene editing, 3206 Medical biotechnology, vector manufacturing and quality control, CRISPR-Cas Systems, extracellular vesicles,
in vivo CRISPR delivery, Life Sciences & Biomedicine, BiotechnologyAccess URL: https://pubmed.ncbi.nlm.nih.gov/40295092
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2
Authors: et al.
Source: EMBO Molecular Medicine. 17:2040-2070
Subject Terms: 3101 Biochemistry and cell biology, HOST, FALCIPARUM, Research & Experimental Medicine, Glucocorticoid Receptor, DOUBLE-BLIND, Mice, Receptors, Glucocorticoid, Nitriles, Animals, MACROPHAGES, PARASITE, CEREBRAL MALARIA, 11 Medical and Health Sciences, SUPPRESSION, Janus Kinases, Mice, Knockout, Inflammation, Science & Technology, 06 Biological Sciences, DISEASE TOLERANCE, GENE, Survival Analysis, Hypoglycemia, Malaria, DEXAMETHASONE, Mice, Inbred C57BL, Disease Models, Animal, Ruxolitinib, Pyrimidines, Glucose, Medicine, Research & Experimental, Liver, Plasmodium chabaudi, Pyrazoles, Cytokines, Tolerance, Life Sciences & Biomedicine, Spleen, Signal Transduction
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3
Authors: et al.
Source: Heald, A H, Reynolds, G, Nash, I, Boyle, O, Daly, C, Longson, D, O'Shea, D, Ingram, J, Holt, R, Firth, J, Stedman, M, Syed, A & de Hert, M 2025, 'Obesity and Schizophrenia : Results of a Feasibility Study with Semaglutide to Assist Weight Loss', Advances in Therapy, vol. 42, pp. 4013–4022. https://doi.org/10.1007/s12325-025-03261-0
Subject Terms: Male, Adult, IMPACT, Glucagon-Like Peptides, 3214 Pharmacology and pharmaceutical sciences, Research & Experimental Medicine, Body Mass Index, Young Adult, PSYCHOSIS, Glucagon-Like Peptide 1, Weight Loss, Humans, Pharmacology & Pharmacy, Obesity, General Clinical Medicine, RISK, Glycated Hemoglobin, Science & Technology, 3202 Clinical sciences, Feasibility, Middle Aged, Treatment, Medicine, Research & Experimental, CARDIOVASCULAR-DISEASE, Schizophrenia, Quality of Life, Feasibility Studies, Female, GAIN, 1115 Pharmacology and Pharmaceutical Sciences, GLP-1, Life Sciences & Biomedicine
Access URL: https://
research .manchester.ac.uk/en/publications/48092340-c7fc-4969-8527-809c37e899ea
https://doi.org/10.1007/s12325-025-03261-0
https://lirias.kuleuven.be/handle/20.500.12942/774328
https://doi.org/10.1007/s12325-025-03261-0 -
4
Authors: et al.
Source: Expert Opinion on Biological Therapy. 25:649-668
Subject Terms: Immunology, Guidelines as Topic, Research & Experimental Medicine, Biologics, COMPARATOR, drug approval, Humans, biosimilars, guidelines, Biosimilar Pharmaceuticals, Drug Approval, 11 Medical and Health Sciences, biosimilarity, Science & Technology, United States Food and Drug Administration, regulation, drug development, STATE, United States, PRODUCTS, Biotechnology & Applied Microbiology, Medicine, Research & Experimental, regulatory assessment, SIMILARITY, EXPERIENCE, 3206 Medical biotechnology, ACCESS, Life Sciences & Biomedicine, CLINICAL-TRIALS, INTELLECTUAL PROPERTY
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Molecular determinants of sotorasib clinical efficacy in KRASG12C-mutated non-small-cell lung cancer
Authors: et al.
Source: Skoulidis, F, Li, B T, de Langen, A J, Hong, D S, Lena, H, Wolf, J, Dy, G K, Curioni Fontecedro, A, Tomasini, P, Velcheti, V, van der Wekken, A J, Dooms, C, Paz-Ares Rodriguez, L, Mountzios, G, Sacher, A, Nadal, E, Couraud, S, Kim, S W, O’Byrne, K, Rocco, D, Toyozawa, R, Chmielewska, I, Lindsay, C R, Hindoyan, A, Mukundan, L, Wilmanski, T, Anderson, A, Ardito-Abraham, C, Pati, A, Reddy, A, Mehta, B & Schuler, M 2025, 'Molecular determinants of sotorasib clinical efficacy in KRAS G12C-mutated non-small-cell lung cancer', Nature Medicine, vol. 31, 110993, pp. 2755–2767. https://doi.org/10.1038/s41591-025-03732-5
Subject Terms: Male, Biochemistry & Molecular Biology, KRAS G12C, Lung Neoplasms, NF-E2-Related Factor 2, Pyridines, Immunology, INHIBITION, Antineoplastic Agents, Docetaxel, Research & Experimental Medicine, Piperazines, MECHANISMS, SUBTYPES, Proto-Oncogene Proteins p21(ras), Carcinoma, Non-Small-Cell Lung, PROGRAM, Humans, HETEROGENEITY, Precision Medicine, MUTATION, 11 Medical and Health Sciences, OUTCOMES, Science & Technology, Kelch-Like ECH-Associated Protein 1, 42 Health sciences, ADAGRASIB, Cell Biology, 32 Biomedical and clinical sciences, Prognosis, DNA-Binding Proteins, Pyrimidines, Treatment Outcome, Medicine, Research & Experimental, Mutation, Female, Life Sciences & Biomedicine, RESISTANCE, Transcription Factors
Access URL: https://
research .manchester.ac.uk/en/publications/f4082985-4762-40fd-9dcd-f0894220e229
https://doi.org/10.1038/s41591-025-03732-5
https://lirias.kuleuven.be/handle/20.500.12942/767540
https://doi.org/10.1038/s41591-025-03732-5
https://research .manchester.ac.uk/en/publications/f4082985-4762-40fd-9dcd-f0894220e229
http://www.scopus.com/inward/record.url?scp=105006913721&partnerID=8YFLogxK
https://doi.org/10.1038/s41591-025-03732-5 -
6
Authors: et al.
Source: Nat Med
Nature medicineSubject Terms: Parents, Biochemistry & Molecular Biology, China, Adolescent, Immunology, Research & Experimental Medicine, CHINA, Article, Humans, KNOWLEDGE, Papillomavirus Vaccines, Child, Biology, 11 Medical and Health Sciences, Science & Technology, Schools, 42 Health sciences, HUMAN-PAPILLOMAVIRUS, Papillomavirus Infections, Vaccination, Cell Biology, 32 Biomedical and clinical sciences, Patient Acceptance of Health Care, Chemistry, Generative Artificial Intelligence, Medicine, Research & Experimental, Female, Human medicine, Life Sciences & Biomedicine
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7
Authors: et al.
Source: Neuromodulation: Technology at the Neural Interface. 28:501-510
Subject Terms: Male, Parkinson's disease, 1702 Cognitive Sciences, Deep Brain Stimulation, Clinical Neurology, DBS, LFP, Research & Experimental Medicine, Globus Pallidus, initial programming, Subthalamic Nucleus, RECORDINGS, Humans, sensing, Retrospective Studies, Aged, GLOBUS-PALLIDUS INTERNUS, Science & Technology, Neurology & Neurosurgery, SUBTHALAMIC NUCLEUS, Neurosciences, 3202 Clinical sciences, 1103 Clinical Sciences, Parkinson Disease, Middle Aged, LOCAL-FIELD POTENTIALS, Treatment Outcome, Medicine, Research & Experimental, 3209 Neurosciences, Feasibility Studies, Female, Neurosciences & Neurology, 1109 Neurosciences, Life Sciences & Biomedicine
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8
Authors: et al.
Source: Neuromodulation: Technology at the Neural Interface. 28:484-491
Subject Terms: Male, DIAGNOSTIC-CRITERIA, 1702 Cognitive Sciences, Deep Brain Stimulation, Clinical Neurology, Research & Experimental Medicine, Neuropsychological Tests, Cognition, Subthalamic Nucleus, Preoperative Care, Humans, Cognitive Dysfunction, Retrospective Studies, Aged, Science & Technology, Neurology & Neurosurgery, motor improvement, SCORES, Neurosciences, 3202 Clinical sciences, 1103 Clinical Sciences, Parkinson Disease, IMPAIRMENT, Middle Aged, deep brain stimulation, Parkinson disease, Treatment Outcome, Medicine, Research & Experimental, 3209 Neurosciences, Female, Neurosciences & Neurology, 1109 Neurosciences, Life Sciences & Biomedicine
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9
Authors: et al.
Source: Curr Mol Med
Subject Terms: 0301 basic medicine, 03 medical and health sciences, 0302 clinical medicine, Life Sciences, Biochemistry, Medicine, Research & Experimental, Biochemistry And Molecular Biology, Molecular Medicine
Access URL: https://pubmed.ncbi.nlm.nih.gov/38213136
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10
Authors: et al.
Source: Nat Med
Subject Terms: Male, Biochemistry & Molecular Biology, OUTBREAK, Sexual Behavior, Immunology, UNITED-STATES, HIV Infections, Research & Experimental Medicine, Article, Disease Outbreaks, HEPATITIS, INFECTION, Humans, NETWORK, Homosexuality, Male, Epidemics, 11 Medical and Health Sciences, Phylogeny, Science & Technology, 42 Health sciences, HIV, Cell Biology, 32 Biomedical and clinical sciences, TIME, Mpox, Monkeypox, Phylogeography, Medicine, Research & Experimental, INCUBATION PERIOD, HIV-1, VIRUS, New York City, Female, JYNNEOS VACCINE, Life Sciences & Biomedicine
Access URL: https://pubmed.ncbi.nlm.nih.gov/40133528
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11
Authors: et al.
Source: Adv Ther
Subject Terms: Adult, Male, Esophageal Neoplasms, 3214 Pharmacology and pharmaceutical sciences, Research & Experimental Medicine, Antibodies, Monoclonal, Humanized, B7-H1 Antigen, Tislelizumab, Double-Blind Method, Esophageal squamous cell carcinoma, Antineoplastic Combined Chemotherapy Protocols, Humans, Pharmacology & Pharmacy, General Clinical Medicine, Aged, Retrospective Studies, Randomized Controlled Trials as Topic, Original Research, Science & Technology, PLACEBO, 3202 Clinical sciences, Middle Aged, PHASE-III, CANCER, Clinical trial, PD-1 inhibitor, Secondary Data Analysis, Medicine, Research & Experimental, Clinical Trials, Phase III as Topic, SURVIVAL, Female, Immunotherapy, Esophageal Squamous Cell Carcinoma, 1115 Pharmacology and Pharmaceutical Sciences, Life Sciences & Biomedicine
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12
Authors: et al.
Source: Exp Mol Med
Experimental and Molecular Medicine, Vol 57, Iss 2, Pp 364-378 (2025)
EXPERIMENTAL AND MOLECULAR MEDICINESubject Terms: EXPRESSION, Biochemistry & Molecular Biology, 3101 Biochemistry and cell biology, Serotonin, HUMAN MONOCYTES, ENTEROENDOCRINE CELLS, QD415-436, Research & Experimental Medicine, Biochemistry, 5-HYDROXYTRYPTAMINE, Article, Monocytes, tumor necrosis, human mucosal tissue, intestinal inflammation, DOPAMINE, Cell Movement, Humans, MACROPHAGES, Intestinal Mucosa, 3404 Medicinal and biomolecular chemistry, Inflammation, Science & Technology, RECEPTOR, 0304 Medicinal and Biomolecular Chemistry, Tumor Necrosis Factor-alpha, Inflammatory Bowel Diseases, CYTOKINE, MICROBIOME, Medicine, Research & Experimental, Medicine, Life Sciences & Biomedicine, STEM-CELLS, Signal Transduction
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Encorafenib, cetuximab and chemotherapy in BRAF-mutant colorectal cancer: a randomized phase 3 trial
Authors: et al.
Contributors: et al.
Source: Nat Med
Scientia
Scientia. Dipòsit d'Informació Digital del Departament de Salut
instnameSubject Terms: Male, Organoplatinum Compounds, TÉCNICAS Y EQUIPOS ANALÍTICOS, DIAGNÓSTICOS Y TERAPÉUTICOS::terapéutica::terapéutica::farmacoterapia::protocolos antineoplásicos::terapéutica::farmacoterapia::protocolos de quimioterapia antineoplásica combinada, Otros calificadores::Otros calificadores::Otros calificadores::/farmacoterapia, Leucovorin, Cetuximab, Research & Experimental Medicine, Còlon - Càncer - Tractament, Antineoplastic Combined Chemotherapy Protocols, MUTATION, 11 Medical and Health Sciences, PLUS CETUXIMAB, Aged, 80 and over, FENÓMENOS Y PROCESOS::fenómenos genéticos::variación genética::mutación, Sulfonamides, Other subheadings::Other subheadings::Other subheadings::/drug therapy, Middle Aged, Progression-Free Survival, Medicine, Research & Experimental, Female, TÉCNICAS Y EQUIPOS ANALÍTICOS, DIAGNÓSTICOS Y TERAPÉUTICOS::diagnóstico::pronóstico::resultado del tratamiento::supervivencia libre de progresión, Fluorouracil, Colorectal Neoplasms, Life Sciences & Biomedicine, Proto-Oncogene Proteins B-raf, Adult, Biochemistry & Molecular Biology, DISEASES::Neoplasms::Neoplasms by Site::Digestive System Neoplasms::Gastrointestinal Neoplasms::Intestinal Neoplasms::Colorectal Neoplasms, ANALYTICAL, DIAGNOSTIC AND THERAPEUTIC TECHNIQUES, AND EQUIPMENT::Therapeutics::Therapeutics::Drug Therapy::Antineoplastic Protocols::Therapeutics::Drug Therapy::Antineoplastic Combined Chemotherapy Protocols, BEVACIZUMAB, Immunology, INHIBITION, ANALYTICAL, DIAGNOSTIC AND THERAPEUTIC TECHNIQUES, AND EQUIPMENT::Diagnosis::Prognosis::Treatment Outcome::Progression-Free Survival, Quimioteràpia combinada, Article, LEUCOVORIN, ENFERMEDADES::neoplasias::neoplasias por localización::neoplasias del sistema digestivo::neoplasias gastrointestinales::neoplasias intestinales::neoplasias colorrectales, Recte - Càncer - Tractament, Humans, COMBINATION, Aged, Science & Technology, 42 Health sciences, Cell Biology, 32 Biomedical and clinical sciences, FLUOROURACIL, 1ST-LINE TREATMENT, Anomalies cromosòmiques, PHENOMENA AND PROCESSES::Genetic Phenomena::Genetic Variation::Mutation, Mutation, Avaluació de resultats (Assistència sanitària), Carbamates
File Description: application/pdf
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Identification of Cell Fate Determining Transcription Factors for Generating Brain Endothelial Cells
Authors: et al.
Source: Stem Cell Rev Rep
Subject Terms: Pluripotent Stem Cells, FIBROBLASTS, Research & Experimental Medicine, Article, BBB Model, PSC, Cell & Tissue Engineering, TARGETS, 10 Technology, Humans, Cell Lineage, 11 Medical and Health Sciences, Science & Technology, 31 Biological sciences, Gene Expression Profiling, Endothelial Cells, Brain, Cell Differentiation, Cell Biology, 06 Biological Sciences, Reprogramming Factors, Medicine, Research & Experimental, Blood brain barrier, Blood-Brain Barrier, BMECs, Differentiation, MARKER, RNA, Transcriptome, Life Sciences & Biomedicine, Developmental Biology, Transcription Factors
Access URL: https://pubmed.ncbi.nlm.nih.gov/39853537
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15
Authors: et al.
Source: Trials. 26
Subject Terms: Male, Probe trabeculotomy, Catheters, Time Factors, SURGERY, 4202 Epidemiology, Trabeculectomy, Research & Experimental Medicine, Childhood glaucoma, General & Internal Medicine, Humans, Multicenter Studies as Topic, Prospective Studies, Child, Congenital glaucoma, 1102 Cardiorespiratory Medicine and Haematology, Intraocular Pressure, Randomized Controlled Trials as Topic, PEDIATRIC GLAUCOMA, Science & Technology, Buphthalmos, 3202 Clinical sciences, Infant, Glaucoma, 1103 Clinical Sciences, 4203 Health services and systems, CONGENITAL GLAUCOMA, Trabeculotomy, Microcatheter-assisted 360° trabeculotomy, Treatment Outcome, Medicine, Research & Experimental, Cardiovascular System & Hematology, Microcatheter-assisted 360 degrees trabeculotomy, Randomized controlled trial, Child, Preschool, Female, Life Sciences & Biomedicine
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16
Authors: et al.
Source: Journal of Inherited Metabolic Disease. 48
Subject Terms: Male, NIEMANN-PICK-DISEASE, Adolescent, organomegaly, Research & Experimental Medicine, Niemann-Pick type A/B, 3105 Genetics, Endocrinology & Metabolism, recombinant human acid sphingomyelinase, Humans, Enzyme Replacement Therapy, Niemann-Pick type B, Child, Genetics & Heredity, lung diffusing capacity, Niemann‐Pick type A/B, Science & Technology, Niemann‐Pick type B, 3202 Clinical sciences, chronic acid sphingomyelinase deficiency, Infant, 1103 Clinical Sciences, NATURAL-HISTORY, Niemann-Pick Disease, Type A, Recombinant Proteins, Sphingomyelin Phosphodiesterase, Treatment Outcome, Medicine, Research & Experimental, Liver, Child, Preschool, dose escalation, Splenomegaly, Female, Life Sciences & Biomedicine, Hepatomegaly
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17
Authors: et al.
Source: Orphanet Journal of Rare Diseases. 20
Subject Terms: Male, Adult, Parents, Adolescent, Research & Experimental Medicine, PHENOTYPE, 3105 Genetics, BEHAVIOR PROBLEMS, Social support, PARENTS, Surveys and Questionnaires, DiGeorge Syndrome, Humans, Child, Genetics & Heredity, Science & Technology, Depression, Mediation, 3202 Clinical sciences, Social Support, Medicine, Research & Experimental, Caregivers, 22q11.2 deletion syndrome, Mental health, Female, Life Sciences & Biomedicine, 1199 Other Medical and Health Sciences
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18
Authors: et al.
Source: Archives of pathology & laboratory medicine.
Subject Terms: Adult, BEVACIZUMAB, BIOMARKERS, Research & Experimental Medicine, Lymphocytes, Tumor-Infiltrating, MUTATION-STATUS, Pathology, Humans, CANCER PATIENTS, Homologous Recombination, Aged, Ovarian Neoplasms, BRCA2 Protein, Science & Technology, BRCA1 Protein, OLAPARIB, 3202 Clinical sciences, 1103 Clinical Sciences, Middle Aged, BRCA1, TUMORS, Cystadenocarcinoma, Serous, Medical Laboratory Technology, MAINTENANCE, Medicine, Research & Experimental, CELLS, Mutation, PATTERNS, Female, Neoplasm Grading, Life Sciences & Biomedicine
Access URL: https://pubmed.ncbi.nlm.nih.gov/39648143
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19
Authors: et al.
Contributors: et al.
Source: NPJ Vaccines
npj VaccinesSubject Terms: HEMODIALYSIS, Coronaviruses, Immunology, 32 Biomedical and Clinical Sciences, Research & Experimental Medicine, Article, Vaccine Related, Clinical Research, Genetics, KIDNEY-TRANSPLANT, MYCOPHENOLATE-MOFETIL, Transplantation, Science & Technology, Prevention, MORTALITY, SIGNATURE, COVID-19, 3 Good Health and Well Being, Organ Transplantation, 3207 Medical microbiology, DIALYSIS PATIENTS, 3204 Immunology, Emerging Infectious Diseases, Infectious Diseases, 3.4 Vaccines, Medicine, Research & Experimental, ANTIBODY, INFLUENZA, SURVIVAL, Immunization, Life Sciences & Biomedicine, Biotechnology
File Description: application/pdf; application/zip; text/xml
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20
Authors: et al.
Source: Orphanet J Rare Dis
Subject Terms: Genetics & Heredity, Health Services Needs and Demand, Science & Technology, Unmet health-related needs, IMPACT, 3202 Clinical sciences, WOMEN, Patient-centred healthcare framework, CHILDREN, Review, Research & Experimental Medicine, ILLNESS, DIAGNOSIS, EXPERIENCES, 3105 Genetics, Rare diseases, Rare Diseases, Medicine, Research & Experimental, PARENTS, Caregivers, QUALITY-OF-LIFE, Humans, BURDEN, Life Sciences & Biomedicine, 1199 Other Medical and Health Sciences
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