Suchergebnisse - "трехплазмидная технология"
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Autoren: et al.
Weitere Verfasser: et al.
Quelle: Biological Products. Prevention, Diagnosis, Treatment; Том 24, № 2 (2024); 123-139 ; БИОпрепараты. Профилактика, диагностика, лечение; Том 24, № 2 (2024); 123-139 ; 2619-1156 ; 2221-996X ; 10.30895/2221-996X-2024-24-2
Schlagwörter: очистка вирусных частиц AAV, gene therapy product, adeno-associated virus, AAV, adeno-associated virus vectors, hereditary diseases, haemophilia, Duchenne muscular dystrophy, gene therapy efficacy, gene therapy safety, AAV production technology, AAV modification, triple-plasmid transfection, AAV-particle purification, генотерапевтический лекарственный препарат, аденоассоциированный вирус, ААV, аденоассоциированные вирусные векторы, наследственные заболевания, гемофилия, миодистрофия Дюшенна, эффективность генной терапии, безопасность генной терапии, технология производства AAV, модификация AAV, трехплазмидная технология
Dateibeschreibung: application/pdf
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